If things go as per plan, in a few months, the US Food and Drug Administration (FDA) will deliberate on the first-of-its-kind CRISPR-based gene therapy for sickle cell disease (SCD) and transfusion-dependent beta thalassemia.

Having made significant advances in a relatively short period of time, CRISPR research is now edging closer to reaching the clinic, and this month’s cover story takes a look at the major players in this field and the big events that could break through this year.

Artificial intelligence (AI) continues to be in the news, and as pharma companies invest more to make sure they’re ahead of the game, international agencies have also started to catch up with regulations for AI-led healthcare research. We also explore how AI is being used to design digital twins for clinical trials.

Also in this issue, we stay on the diversity beat and explore how trials can be more inclusive when it comes to participants with cognitive impairments.

Read the latest issue of Pharma Technology Focus for all this and more news, insights, and analysis from the pharmaceutical industry.

You can also subscribe here to receive email notifications when a new issue is available.

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This content was updated on 25 January 2024