Rethinking Clinical Trials

SEPTEMBER 16, 2022

University of Pennsylvania Perelman School of Medicine. Dr. Joffe and his collaborators conducted a preliminary study of qualitative interviews, funded by PCORI, with 99 leaders of 16 geographically diverse Learning Health Systems. They place a high value on external funding that their faculty bring into the institution.

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Clinical Trials Clinical Trials Trials Research 100

pharmaphorum

JANUARY 21, 2022

Access to medicines is “one of the most challenging policy areas in every country in the European region” – it’s time to develop a solution that works for everyone. Balancing the incentivisation of innovation against affordable access to revolutionary new medicines is an age-old conundrum in the biopharmaceutical industry.

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Medicine Marketing Manufacturing Production 52

pharmaphorum

JUNE 2, 2021

NICE has rejected routine NHS funding for Roche’s Evrysdi (risdiplam) for spinal muscular atrophy drug in draft guidance, a decision which doesn’t come as a surprise to patient association SMA UK. “NICE’s initial ‘no’ to approving risdiplam for NHS funding is not unexpected,” said SMA UK this morning.

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pharmaphorum

AUGUST 28, 2020

Prof Brownstein, who is also chief innovation officer at Boston Children’s Hospital, said: “COVID-19 has put a real focus on the inadequacies of public health. Established with funding from the National Library of Medicine (NLM), it pulls data from sources including news stories, blogs, social media, and chat rooms. “We

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Medicine Research 63

XTalks

FEBRUARY 27, 2024

Despite high price tags of a couple of million dollars, gene therapy makers say they are working to ensure patients are able to access the treatments through patient assistance programs developed in conjunction with the support of governments. Sarepta hopes to clarify Elvidys’ effectiveness in older children in a confirmatory trial.

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Research Drugs Gene Therapy Clinical Trials 59

XTalks

DECEMBER 21, 2022

The past year has been a strong one for life sciences industries, from pivotal gene therapy approvals to continued innovations in the biotech and medical device spaces. Personalized Medicine. There was a significant rise in the number of precision-based medicines like gene therapies and immunotherapies that were approved this year.

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Life Science Gene Therapy Gene Clinical Trials 52

The Pharma Data

NOVEMBER 15, 2020

Peng Liang , Founder and Chief Scientific Officer of Clover and inventor of the Trimer-Tag© technology, says, “A successful vaccine that can truly modulate the course of the COVID-19 pandemic must have four essential characteristics: safety, efficacy, scalability of manufacturing, and speed. Know more about us on www.cytiva.com.

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Vaccination Vaccine Manufacturing Life Science 52