pharmaphorum

JANUARY 11, 2021

While bluebird has conducted pioneering work in gene therapy for blood disorders and in cancer cell therapy, products have been delayed by issues with filing data for the FDA. million price tag. Meanwhile the as-yet unnamed oncology company will spin off under the leadership of bluebird’s current chief executive Nick Leschly.

Gene Therapy 58

Gene Therapy Gene Genetic Disease Manufacturing 58

Pharmaceutical Technology

APRIL 5, 2023

But access to these treatments continues to remain limited due to high price tags and variable availability across regions. This includes the first potential approval of a CRISPR-based gene therapy called exa-cel , which is developed by CRISPR Therapeutics and Vertex Pharmaceuticals. How has the field changed in recent years?

Gene Therapy 147

Gene Therapy Gene Engineer Production 147

XTalks

FEBRUARY 27, 2024

Given the significant unmet needs in the advanced melanoma community, we are proud to offer a personalized, one-time therapeutic option for these patients.” Addressing the high price tag, Iovance’s commercial chief Jim Ziegler said, “Payers have expressed their appreciation for the value proposition for Amtagvi.”

FDA Approval 52

FDA Approval Manufacturing In-Vivo Trials 52

XTalks

FEBRUARY 27, 2024

With the approval, Vertex Pharmaceuticals and CRISPR Therapeutics’ jointly developed Casgevy also became the first CRISPR/Cas9-based therapy approved in the US. Developed by Sarepta Therapeutics, the therapy is approved for ambulatory children four to five years of age with DMD who have a confirmed mutation in the dystrophin gene.

Research 59

Research Drugs Gene Therapy Clinical Trials 59

XTalks

JANUARY 19, 2024

Therapeutic radiopharmaceuticals are particularly used in the treatment of cancer. Therapeutic radiopharmaceuticals deliver beta or alpha radiation, which destroys diseased cells, such as cancer cells. billion influx into radiopharmaceuticals which underscores the potential and robust growth in this therapeutic area.

DNA 66

DNA Radiology FDA Approval Development 66

Delveinsight

DECEMBER 3, 2020

Roche has got an authorization from the FDA for a more accurate COVID-19 blood test capable of measuring the levels of specific antibodies, which target the cell-unlocking spike protein of coronavirus. He also estimates that the global sternal closure business is currently increasing by high single-digit percentages each year.

Gene Therapy 52

Gene Therapy Gene Antibody Research 52

Pharmaceutical Technology

NOVEMBER 30, 2022

However, there has recently been a boom in interest and research in anti-obesity therapeutics. Anti-obesity therapeutic landscape. The company’s weight loss drug Saxenda (liraglutide) won an approval for chronic weight management in December 2014, and Wegovy (semaglude) got the same tag in 2021. compared to a 5.1%

Drugs 264

Drugs Manufacturing Hormones Contract Manufacturing 264