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Novartis’ $2 Million Gene Therapy Zolgensma Shows ‘Remarkable’ Results and Offers Hope for Children with SMA

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With a price tag of over $2.5 Mendell, MD, attending neurologist at Nationwide Children’s Hospital in Ohio and lead author on the study, said in an interview with Healio Neurology. million, Zolgensma is currently the world’s most expensive drug. It was first approved in the US in 2019 to treat children below the age of two with SMA.