Pharmaceutical Technology

JUNE 29, 2022

For example, while orphan drug designations have more than doubled in the last decade compared to the previous one, only 16% of therapies with orphan tags have managed to gain FDA approval in some indications. What happens after a drug gets an orphan drug designation?

Drugs 246

Drugs FDA Approval Marketing Development 246

XTalks

DECEMBER 21, 2022

The multi-million-dollar price tags are largely attributable to the high R&D and manufacturing costs associated with making a gene therapy, as the raw materials for producing the therapy can be expensive. Personalized Medicine. New age neurostimulation devices to treat also offer patients personalized treatment.

Life Science 52

Life Science Gene Therapy Gene Clinical Trials 52

Rethinking Clinical Trials

DECEMBER 6, 2022

Professor of Medicine. In the intervention group patients received 3 text messages weekly that were personalized encouraging them to be more active based on the past week’s activity.                                           . Speakers. Michael Felker, MD, MHS. Key Points.

Trials 130

Trials Clinical Trials Clinical Trials Compliance 130

Rethinking Clinical Trials

OCTOBER 27, 2022

Duke University School of Medicine . Having a tech person on the study design team to advise on which devices are secure will allow as many people as possible to participate. Chief Science & Digital Officer. Duke Clinical Research Institute. Professor, Department of Population Health Sciences. Chief Research Technology Strategist.

Clinical Research 130

Clinical Research Research Clinical Trials Clinical Trials 130

Pharmaceutical Technology

APRIL 5, 2023

But access to these treatments continues to remain limited due to high price tags and variable availability across regions. We have the emergence of this new pillar of medicine, which is out of the lab and beyond clinical trials now.

Gene Therapy 147

Gene Therapy Gene Engineer Production 147

XTalks

FEBRUARY 27, 2024

Despite high price tags of a couple of million dollars, gene therapy makers say they are working to ensure patients are able to access the treatments through patient assistance programs developed in conjunction with the support of governments. Sarepta hopes to clarify Elvidys’ effectiveness in older children in a confirmatory trial.

Research 59

Research Drugs Gene Therapy Clinical Trials 59

Rethinking Clinical Trials

SEPTEMBER 21, 2023

I think there’s probably a lot of people here who know how difficult it is to recruit people in person. Discussion Themes – Compared to some of the other work that you and your colleague shave done, would you describe this as easier to do since you’re taking advantage of online approaches, or was it harder?

Clinical Trials 130

Clinical Trials Clinical Trials Sales Trials 130

pharmaphorum

JANUARY 31, 2023

Medication is a staple of modern medicine, with almost 50% of adults in the United States taking at least one prescription medication. Given the high price tags placed on many medications, it’s easy to understand why patients often feel that they are being taken advantage of.

Clinical Trials 52

Clinical Trials Clinical Trials Trials Vaccination 52

XTalks

JANUARY 19, 2024

Radiobiological and Clinical Considerations from CRO and Emerging Biotech Radiopharmaceuticals are medicinal formulations containing radioisotopes that are used in the field of nuclear medicine primarily for the diagnosis and treatment of various diseases, particularly cancer. There have been more than $1.7

DNA 66

DNA Radiology FDA Approval Development 66

The Pharma Data

OCTOBER 9, 2021

This designation is predicated on data showing that gantenerumab significantly reduced brain amyloid pillar, a pathological hallmark of Notice, in the ongoing SCarlet RoAD and Marguerite RoAD open- tag extension trials, as well as other studies.

Antibody 52

Antibody In-Vitro Trials Development 52

Pharmaceutical Technology

JUNE 21, 2023

The high price tag may be hard to defend , but with lifetime treatment costs for haemophilia B reaching as high as $23m for some, the single-dose treatment could prove far more cost-effective. Despite the limited market, the price tags of haemophilia make it potentially lucrative. Haemophilia B is a rare condition.

Gene Therapy 246

Gene Therapy Gene Sales Protein 246

The Pharma Data

MAY 15, 2021

While this can be a great motivator for personal use…. Most importantly, despite the fact that mainstream medicine does have its place, I always seek to find natural, drug-free solutions to even the most pressing health issues. At the end of the day, this data is sent to various computers which give you a detailed report to look at.

Production 52

Production Containment Medicine Vaccination 52

XTalks

FEBRUARY 11, 2021

This has ushered in a new era of genomics that is fostering rapid, detailed and personalized insights into human genetics. It is often reported that Franklin and Wilkins had contrasting personalities, with Franklin being strongly and vocally opinionated compared to the quieter Wilkins, who disliked arguments and “rocking the boat,” so to say.

Genetics 119

Genetics DNA Genome Genomics 119