pharmaphorum

OCTOBER 3, 2022

Amylyx Pharmaceuticals’ Relyvrio – a new treatment for amyotrophic lateral sclerosis (ALS) approved by the FDA on Thursday, after review of the data from its phase 2 trial – was the next day set at a list price of $158,000 per year in the US, sparking outcry. ALS affects over 30,000 people in the US.

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Pharmaceutical Technology

JUNE 23, 2023

Sarepta will now need to complete a confirmatory trial to prove the therapy improves physical function and mobility.

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Gene Therapy FDA Approval Gene Trials 130

Fierce Pharma

MARCH 20, 2024

Kyowa Kirin and its subsidiary Orchard Therapeutics have broken new boundaries in pricing, too. After scoring an FDA nod Monday for the first gene therapy to treat the rare genetic disease metachromatic leukodystrophy (MLD) in the U.S.,

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Gene Therapy Gene Genetic Disease Genetics 129

Bio Pharma Dive

AUGUST 28, 2020

A draft report from the drug pricing watchdog concluded that, under the right conditions, Roctavian may be cost-effective at a price of $2.5

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Gene Therapy Gene Drugs 300

pharmaphorum

MARCH 20, 2024

Orchard Therapeutics has revealed the US price of Lenmeldy, its gene therapy for rare disease MLD, placing a $4.25m price tag on the one-shot treatment

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Gene Therapy Gene Medicine 110

pharmaphorum

JUNE 8, 2021

.” Biogen meanwhile has been taking flak over its decision to price Aduhelm at $56,000 per year, which looks set to re-ignite debate in the US about the cost of medicines. Aside from the high price, another issue is its dosing by monthly infusion, as clinics that can provide this are not available in all areas. billion in 2027.

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Pharmaceutical Technology

JULY 14, 2023

Yusimry is priced at $995 per carton of two autoinjectors compared to Humira’s price tag of $6,922 for the same quantity.

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Sales 130

Bio Pharma Dive

FEBRUARY 25, 2021

Like other Sarepta drugs, it comes with a high price tag and its clinical benefits haven't been confirmed. Amondys 45 is now cleared for the estimated 8% of Duchenne patients eligible for treatment.

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FDA Approval Drugs 275

BioSpace

NOVEMBER 21, 2023

What can patients expect the price tag to be? CRISPR gene-editing has had its first ever approval in the UK. Will the FDA follow suit?

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Gene Therapy Gene Editing Gene 125

Medical Xpress

APRIL 26, 2023

Menopause-related symptoms such as hot flashes, night sweats, mood changes, sleep disturbances, joint aches and cognitive difficulties damage the quality of life for millions of women. They also can adversely affect women in the workplace. A newly published Mayo Clinic study puts numbers on that cost: an estimated $1.8

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Fierce Pharma

JULY 14, 2023

The potentially curative promise of gene therapies often carries a steep price tag. | The potentially curative promise of gene therapies often carries a steep price tag. But for a pair of personalized medicine prospects in sickle cell disease (SCD), the cost could be worth it, at least as far as ICER is concerned.

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Gene Therapy Gene Medicine 98

Pharmaceutical Technology

SEPTEMBER 30, 2022

Spark Therapeutics’ Luxturna, indicated for inherited retinal disease (IRD), was the first gene therapy to be approved, in 2017, with a price tag of $850,000 for each eye. bluebird then broke its own pricing record when the $3m Skysona was approved, and now faces the unique challenge of selling the world's two most expensive drugs.

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Gene Therapy FDA Approval Gene Genetic Disease 289

Bio Pharma Dive

JUNE 30, 2021

But if some efficacy is assumed, ICER argues Biogen's $56,000 price tag is far too high. The influential nonprofit maintains that the clinical trial evidence supporting Aduhelm is insufficient to prove a health benefit.

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Clinical Trials Clinical Trials Trials 180

Fierce Pharma

NOVEMBER 7, 2023

One potential advantage for bluebird, giving the timing, could be a chance to view its rival's pricing before deciding itself. But on Tuesday bluebird said that Vertex’s price tag will not factor into how the Massachusetts company will price its treatment.

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Gene Therapy Gene 113

Pharmaceutical Commerce

MARCH 6, 2024

Navigating the complex landscape of healthcare coverage can be an intimidating task, especially for patients with rare diseases for which treatments often come with a high price tag.

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BioSpace

NOVEMBER 7, 2023

Cell and gene therapy represents the most promising breakthrough in cancer treatment for decades, but it comes with a hefty price tag. Here’s how to drive costs down.

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Gene Therapy Gene 81

Medical Xpress

APRIL 21, 2023

The life-saving drug "Narcan" is expected to be available over-the-counter later this year, but its price tag is expected to put it out of reach for many below the poverty line.

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Drugs 98

Scienmag

JUNE 19, 2022

So far, science has described more than 2 million species, and millions more await discovery. While species have value in themselves, many also deliver important ecosystem services to humanity, such as insects that pollinate our crops.

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Scientist Marketing 69

NPR Health - Shots

OCTOBER 15, 2022

The $100 price tag is too much for the poor. Public hospitals in Liberia may require a bag of supplies to gain admission for delivery: bleach, baby clothes, diapers. One nurse has a solution. Image credit: Joel R.

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Nurses 115

STAT News

MARCH 10, 2023

By law, Medicare will have to take a medication’s efficacy and its research and development costs into account when it starts to negotiate drug prices — but recent research shows pharma companies ignore those factors when they pick prices for their products. But neither factor has much effect, the studies concluded.

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Drugs Pharma Companies Research Production 98

STAT News

OCTOBER 27, 2022

Amid sporadic shortages of a drug that is essential in preparing patients for lifesaving, cancer-fighting treatments, one manufacturer has returned to the market — but is selling its medicine for 10 to 20 times the prices offered by the only other companies with available supplies. Continue to STAT+ to read the full story…

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Medicine Manufacturing Marketing Drugs 111

XTalks

MARCH 25, 2024

The Root of the Chocolate Shortage For the past three years, the cocoa industry has grappled with underwhelming harvests, significantly driving up prices. These price hikes have put immense pressure on cocoa processors, critical in converting cocoa beans into cocoa butter and liquor for global chocolate production.

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Production Manufacturing Branding Marketing 110

Pharmaceutical Technology

FEBRUARY 10, 2023

On November 22, 2022, the FDA approved CSL Behring’s Hemgenix (etranacogene dezaparvovec), the first gene therapy treatment for hemophilia B, with a staggering manufacturer price of $3.5 million, according to GlobalData’s Price Intelligence (POLI), making it the most expensive drug in the world.

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Gene Therapy Marketing Gene Drugs 263

STAT News

JANUARY 6, 2023

Such decisions are based on myriad factors, starting with the average $26,500 price tag. Food and Drug Administration has granted accelerated approval to the widely anticipated Alzheimer’s drug from Eisai and Biogen, a key question is the extent to which payers — private and public — will cover the treatment.

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Medical Xpress

MARCH 8, 2023

Failure to enroll enough participants in trials can delay the arrival of new therapies in the clinic and inflate their eventual price tags. Before new therapies can reach patients, they must be tested in clinical trials in representative populations to show that they work and are safe.

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Clinical Trials Clinical Trials Trials Drugs 105

World of DTC Marketing

JULY 20, 2022

have raised drug prices 1,186 times so far this year. Patients for Affordable Drugs found that between June 24 and July 5, pharmaceutical companies increased prices for 133 products. Pfizer, for instance, hiked the cost of its leukemia medication Besponsa again this month, bringing its per-vial price tag to $21,056.

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Packaging Packaging Drugs Vaccination 183

Pharmaceutical Technology

MAY 19, 2023

DMTs for MS have a high price tag, particularly in the US. A similar trend of price increases was also seen for MS generics and biosimilars. However, they cannot provide a cure and have a very limited impact on halting disease progression.

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STAT News

DECEMBER 13, 2022

argued the planned price tag is nearly four times the current $30 price paid by the U.S. A pair of U.S. ” In their letter, U.S. Elizabeth Warren (D-Mass.) Peter Welch (D-Vt.) government and also represents a 10,000% markup over what some researchers have calculated as the cost to produce the vaccine.

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Vaccination Vaccine Research Drugs 98

Medical Xpress

NOVEMBER 23, 2022

million price tag. People with one form of the genetic blood disorder hemophilia now have a one-time treatment with a $3.5

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Gene Therapy FDA Approval Gene Genetics 74

BioSpace

JULY 11, 2021

Adulhelm's proposed price tag of $56,000 per patient per year is hardly the most expensive drug on the market, but controversy regarding packaging and pricing continues.

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Packaging Packaging Marketing Drugs 78

STAT News

AUGUST 16, 2022

per cartridge, a reduction from the previous price tag of $16.86. At issue is a TB test developed by Cepheid, which reached a 10-year deal with the WHO in August 2012 to supply its GeneXpert diagnostic to dozens of low- and middle-income countries. In exchange for $11.1 Continue to STAT+ to read the full story…

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Production Development Drugs 119

STAT News

MARCH 10, 2023

Enjoy, and see you soon … By law, Medicare will have to take a medication’s efficacy and its research and development costs into account when it starts to negotiate drug prices — but recent research shows pharma companies ignore those factors when they pick prices for their products , STAT explains. Two

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Insulin Pharmacy Pharma Companies Drugs 96

STAT News

JULY 14, 2022

These treatments constitute a highly lucrative market because they are used to help the body fight cancer, infection, and a wide array of other diseases — and often carry considerable price tags. Continue to STAT+ to read the full story…

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Medicine Marketing Drugs 98

STAT News

AUGUST 17, 2022

Attorneys for the counties put the total price tag at $3 billion for the damage done to the counties. District Judge Dan Polster said in the ruling that the money will be used to abate a continuing opioid crisis in Lake and Trumbull counties, outside Cleveland. Read the rest…

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Pharmacy 98

Scienmag

JULY 4, 2022

Government policies often are presented with hefty price tags, but people often zone out as more zeros are added to the total cost.

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Pharmaceutical Commerce

AUGUST 1, 2022

Price tag for bivalent dose was $1.74 billion.

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World of DTC Marketing

SEPTEMBER 9, 2021

SUMMARY: Allowing Medicare to negotiate drug prices is popular with voters because the media has been focused on the high price of some drugs, but this measure won’t lead to lower healthcare costs. Generally, healthcare prices are higher in the U.S. healthcare spending will reach $6.2 healthcare. healthcare spending.

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