XTalks

JUNE 8, 2021

Novartis’ Zolgensma (onasemnogene abeparvovec) gene therapy has been making significant strides as of late, including dosing of the first Spinal Muscular Atrophy (SMA) patient with the treatment in the UK last week. With a price tag of over $2.5 Baby Arthur: First UK Patient. Zolgensma Gene Therapy: START Trial.

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Gene Therapy Gene Protein Trials 110

pharmaphorum

DECEMBER 2, 2020

This expertise in fermentation and large-scale pharmaceutical production put Pfizer in good stead when in 1941 the US government appealed to the pharma industry for support in producing penicillin for the war effort. For all the latest Pfizer news follow pharmaphorum’s Pfizer tag.

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Sales Production Drugs Marketing 128

XTalks

FEBRUARY 27, 2024

Despite high price tags of a couple of million dollars, gene therapy makers say they are working to ensure patients are able to access the treatments through patient assistance programs developed in conjunction with the support of governments. Sarepta hopes to clarify Elvidys’ effectiveness in older children in a confirmatory trial.

Research 59

Research Drugs Gene Therapy Clinical Trials 59

The Pharma Data

MAY 5, 2021

UK Spinraza Data Review Shows Benefits Of NICE Flexibility ( Pink Sheet ). AbbVie’s Humira regains top pharma TV spender spot, while sibling brands Rinvoq and Skyrizi tag along ( Fierce ). Government & Regulatory. Government & Regulatory. Medtech.

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Vaccination Vaccine Gene Therapy Contract Packaging 52