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Can gene therapies for haemophilia defend their high price tags?

Pharmaceutical Technology

million price tag. But the justification for Roctavian’s cost will depend on positive responses to the treatment, says Dr. Guy Young, professor of pediatrics at University of Southern California’s Keck School of Medicine. The post Can gene therapies for haemophilia defend their high price tags? million ($1.8

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Grand Rounds October 27, 2023: Digital, Decentralized and Democratized: Lessons From The Yale PaxLC Trial (Harlan M. Krumholz, MD, SM)

Rethinking Clinical Trials

Using the local Yale IRB was an asset. The Yale IRB and Trusted Medical helped facilitate the other states and anything we need to take in account for recruitment. Tags #pctGR, @Collaboratory1 The post Grand Rounds October 27, 2023: Digital, Decentralized and Democratized: Lessons From The Yale PaxLC Trial (Harlan M.

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