Richard Horgan has waited for this moment for more than three years.
Last month, the Food and Drug Administration granted permission for his younger brother Terry, 27, who lives with muscular dystrophy, to receive a first-of-its-kind gene therapy that was tailor-made for his genetic mutation.
When the infusion of the drug happens at UMass Chan Medical School, it will be an emotional moment for Terry and Richard, the driving force behind the experimental drug.
This article is exclusive to STAT+ subscribers
Unlock this article — plus daily coverage and analysis of the biotech sector — by subscribing to STAT+.
Already have an account? Log in
Already have an account? Log in
To submit a correction request, please visit our Contact Us page.
STAT encourages you to share your voice. We welcome your commentary, criticism, and expertise on our subscriber-only platform, STAT+ Connect