FDA Action Alert: Vertex/CRISPR, Arcutis and Optinose
BioSpace
DECEMBER 3, 2023
This week, the FDA could approve the first CRISPR-edited therapy in the U.S., while two other companies await decisions on topical drugs.
BioSpace
DECEMBER 3, 2023
This week, the FDA could approve the first CRISPR-edited therapy in the U.S., while two other companies await decisions on topical drugs.
Pharmaceutical Technology
MARCH 28, 2023
Vertex Pharmaceuticals has signed a new non-exclusive licensing agreement with CRISPR Therapeutics to expedite the development of its hypoimmune cell therapies to treat type 1 diabetes (T1D). It originated under the partnership of CRISPR Therapeutics and ViaCyte. Topic sponsors are not involved in the creation of editorial content.
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Pharmaceutical Technology
APRIL 28, 2023
EDIT-301 is made of patient-derived CD34+ haematopoietic stem and progenitor cells, which are edited using CRISPR at the gamma globin gene (HBG1 and HBG2) promoter sites using a proprietary engineered AsCas12a nuclease, per the company’s website. Topic sponsors are not involved in the creation of editorial content.
Pharmaceutical Technology
SEPTEMBER 29, 2022
Scribe Therapeutics and Sanofi have signed a strategic partnership to expedite the development of breakthrough clustered regularly interspaced short palindromic repeats (CRISPR)-based cell therapies for cancer. Topic sponsors are not involved in the creation of editorial content.
Pharmaceutical Technology
MAY 3, 2023
BrightPath will obtain non-exclusive rights to the STAR-CRISPR editing platform of Artisan Bio for accelerating the development of BrightPath’s iNKT cells. Topic sponsors are not involved in the creation of editorial content. Cell & Gene Therapy coverage on Pharmaceutical Technology is supported by Cytiva.
Pharmaceutical Technology
JULY 12, 2022
Furthermore, through the takeover, Vertex will obtain access to new hypoimmune stem cell assets under the ViaCyte-CRISPR Therapeutics partnership. Topic sponsors are not involved in the creation of editorial content. Cell & Gene Therapy coverage on Pharmaceutical Technology is supported by Cytiva.
Pharmaceutical Technology
APRIL 25, 2023
The BLA filing brings bluebird closer to its competitors CRISPR Therapeutics and Vertex Pharmaceuticals , which finished a rolling BLA for their CRISPR-based gene therapy exa-cel for the same condition earlier this month. Topic sponsors are not involved in the creation of editorial content.
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