Remove Gene Silencing Remove Genotype Remove HR Remove RNA
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FDA Approves Oxlumo (lumasiran) for the Treatment of Primary Hyperoxaluria Type 1

The Pharma Data

0.514 mmol/24 hr/1.73 0.771 mmol/24 hr/1.73 Oxlumo works by degrading HAO1 messenger RNA and reducing the synthesis of GO, which inhibits hepatic production of oxalate – the toxic metabolite responsible for the clinical manifestations of PH1. Visit OXLUMO.com for more information, including full Prescribing Information.