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Unlocking the potential of mRNA for the future treatment of rare diseases 

Drug Discovery World

Arcturus Therapeutics has one rare disease program focused on ornithine transcarbamylase deficiency in Phase II clinical study, as well as a preclinical program to investigate an mRNA medicine for cystic fibrosis. She is passionate about advancing research in the pursuit of healthier lives for all.

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Precision cancer therapies: Where are we?

Drug Discovery World

Positive early signs for precision cancer therapies In the first presentation, Dr Fiona McLaughlin, CSO, provided an update on Avacta’s oncology candidates that are currently in clinical development. She explained the mechanism by which AVA6000 can provide more precise treatment than current chemotherapies.

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