The Pharma Data

AUGUST 15, 2021

Food and Drug Administration (FDA) has granted Fast Track designation to VTX-801, Vivet’s clinical-stage gene therapy for the treatment of Wilson Disease – a rare, genetic disorder that reduces the ability of the liver and other tissues to regulate copper levels, causing severe hepatic damage, neurological symptoms, and potentially death.

Gene Therapy 52

Gene Therapy Gene Clinical Trials Clinical Trials 52

Drug Discovery World

MARCH 13, 2023

Drug discovery researchers usually partner with a CDMO to provide support through the development, manufacturing, and clinical supply required to bring a drug to market. CDMOs that integrate digital solutions into their business processes minimise the amount of hands-on work in their operations.

Gene Therapy 52

Gene Therapy Gene Manufacturing Development 52

Drug Discovery World

NOVEMBER 3, 2022

The number of therapy classes in development has exploded as research has advanced methods for tackling a vast array of genetic conditions and diseases in both rare disease and common indications. This change in science demands a change in the supply chain to match. 15 years later . References .

Gene Therapy 52

Gene Therapy Production Development Business Development 52

Pharmaceutical Technology

MARCH 20, 2023

Research suggests that sub-Saharan Africa is expected to see one of the largest global increases in mortality rates caused by non-communicable diseases. However, Africa currently accounts for a very low percentage of global clinical trials, with estimates putting it at approximately 2.5%. “The being African American, 3.4%

Clinical Trials 130

Clinical Trials Clinical Trials Trials Clinical Supply Chain 130