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What Do Patients Have to Say about Gene Therapy Trials? An Upcoming FDA Public Meeting to Hear from Patients and Caregivers

FDA Law Blog

Who better than people living with a condition to inform drug companies, physicians, academics, and the FDA on what it is like to live with their condition, what symptoms most impact their lives, what goes into their decision about whether to participate in a clinical trial, and what kind of treatment effects would be most meaningful to them?

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Blood Donor Day 2023: Experts weigh inĀ 

Drug Discovery World

One example we are following with anticipation are the two FDA approvals for the first gene therapies for sickle cell disease. It enables development and production of Advanced Therapies by providing access to human cells and tissue, testing services and biomanufacturing and clinical trials support.