FDA Approves First Drug to Improve Growth in Children with Most Common Form of Dwarfism
The Pharma Data
NOVEMBER 21, 2021
The FDA approved Voxzogo under the accelerated approval pathway, which allows for earlier approval of drugs that treat serious conditions and fill an unmet medical need, based on a surrogate or intermediate clinical endpoint. 3] Achondroplasia is caused by mutations in the FGFR3 gene. Inheritance is autosomal dominant.[1][2]
Let's personalize your content