Gene Gene Silencing Hormones Pharma Companies 
Delveinsight
AUGUST 6, 2020
Transthyretin (TTR) is a protein that the liver produces to facilitate the transfer of thyroid hormone and vitamin A in the blood. Hereditary ATTR amyloidosis , also known as Familial ATTR, is an autosomal dominant disease and a result of mutations in the TTR gene, thus it is passed down from one generation to the next one.
pharmaphorum
DECEMBER 23, 2020
The results also suggest further uses for the drug in early disease and more revenues to come from one of the company’s biggest success stories from the last decade. The company’s menopause drug NT-814 is heading for phase 3 development in 2021 following a mid-stage trial readout. Rare disease progress.
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