Bluebird Bio’s Skysona Receives FDA Approval and Becomes World’s Most Expensive Drug
XTalks
SEPTEMBER 27, 2022
The record-breaking price tag of Skysona is not surprising for one-time gene therapies like it. Symptoms of CALD typically appear in childhood (median age seven). Related: Bluebird’s $2.8M Gene Therapy Zynteglo Wins Landmark FDA Approval for Beta Thalassemia. Together, this amounts to about 40 cases a year in the US.
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