Remove tag hemlibra
article thumbnail

Can gene therapies for haemophilia defend their high price tags?

Pharmaceutical Technology

million price tag. Both factor VIII prophylactics and Roche’s bispecific antibody Hemlibra that are used for haemophilia A patients are expensive, and so a gene therapy could save money, says Dr. David Rind, chief medical officer (CMO) of ICER. But the case becomes more complicated when it comes to comparisons with Hemlibra.

article thumbnail

Roctavian okay sets up another gene therapy test for Europe

pharmaphorum

BioMarin will no doubt have an eye on the earlier experience of bluebird bio, which secured EU approval for rare disease gene therapy Zynteglo (betibeglogene autotemcel) in 2019 for beta thalassaemia with a price tag of around €1.6 million spread over five years.