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Novartis’ $2 Million Gene Therapy Zolgensma Shows ‘Remarkable’ Results and Offers Hope for Children with SMA

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With a price tag of over $2.5 There are four main types of SMA — type 0 to IV — with type I being the most common and severe form of the disease. In England, five-month old baby Arthur became the country’s first SMA patient to receive the Zolgensma gene therapy last week through the National Health Service (NHS).