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Grand Rounds March 1, 2024: Effect of an Intensive Food-As-Medicine Program on Health and Health Care Use: Evidence from a Randomized Clinical Trial (Joseph Doyle, PhD)

Rethinking Clinical Trials

The intervention group started the program now. The control group started in 6 months and received a brochure that lists addresses of area food banks. Lab results for HbA1c, cholesterol, triglycerides, blood pressure, weight were taken at 0, 6 and 12 months. The treatment group started with a mean 10.3

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Novartis’ $2 Million Gene Therapy Zolgensma Shows ‘Remarkable’ Results and Offers Hope for Children with SMA

XTalks

With a price tag of over $2.5 There are four main types of SMA — type 0 to IV — with type I being the most common and severe form of the disease. While there are typically two copies of the SMN1 gene in a cell, the numbers of SMN2 can vary, with some people having up to eight copies. Zolgensma Gene Therapy: START Trial.

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Second unanimous FDA adcomm vote boosts bluebird bio

pharmaphorum

bluebird bio started last week on tenterhooks, as FDA advisors cast their eyes over data for two gene therapy candidates that are key to its future as a commercially viable concern. Beti-cel has already been approved for marketing in Europe as Zynteglo, with a price tag of around $1.8