Remove Genetic Analysis Remove Genetic Disease Remove Protein Remove RNA
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Unlocking the potential of mRNA for the future treatment of rare diseases 

Drug Discovery World

mRNA enables the delivery of a transiently expressed genetic molecule that is translated into a target protein using the machinery of the host cell. Therefore, the risk for off-target insertional mutagenesis is greatly reduced. In addition, it may be easier to target the therapeutic molecule to the correct cell or tissue.