Remove Immune Response Remove In-Vivo Remove Reagent Remove RNA
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Delivering on the promise of gene editing

Drug Discovery World

Prime editing, while also employing a single strand nick, expands this scope to all 12 possible changes using a more complex prime editing guide RNA (pegRNA). Improve delivery: Clinical translation of gene therapy is dependent on the efficient and safe delivery of gene editing tools into cells, and this can occur either ex vivo or in vivo.