Remove tag exploring-rare-diseases
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Immunocore’s Kimmtrak Gets FDA Approval as First Treatment for Rare Eye Cancer and First T Cell Receptor Therapeutic

XTalks

Uveal melanoma is a rare and aggressive type of melanoma of the eye. Up to 50 percent of patients will develop metastatic disease, mainly spreading to the liver, making treatment difficult and limited. The new treatment will thus help address the unmet need for the disease. The median treatment time is about 23 weeks (or 5.3

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AI-Powered Precision Engagement in Commercial and Medical Functions

Intouch Solutions

This can make a difference in all cases, but particularly with rare diseases. Offering the physician support from a virtual assistant during the differential diagnosis process where they have access to a more extensive knowledge and experience base.

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Pharma By The Numbers: A Retrospective Look at the Industry and 20 Years of Xtalks History

XTalks

The years that followed have seen a rise in large pharma companies acquiring much smaller biopharmas with a narrow focus on rare disease therapeutic development. Click on the infographic to explore the data. And a decade earlier, in 2002, Pfizer’s Lipitor (atorvastatin calcium) reigned supreme.

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Sanofi offers refunds for Cablivi in novel model for rebates

Pharmaceutical Technology

On January 18, Sanofi launched a new warranty program for its rare blood disorder drug Cablivi (caplacizumab), which tackles value-based agreements in a slightly different way. A refund up to 12 inpatient doses will also be offered for patients whose disease worsens while receiving treatment.