tag geographic-atrophy 
pharmaphorum
JANUARY 9, 2023
Novartis’ programme providing free access to its spinal muscular atrophy (SMA) gene therapy Zolgensma is being scaled back to a dozen countries worldwide, according to the company. ” Zolgensma is one of the most expensive therapies available, with a price tag of around $2.1
Delveinsight
DECEMBER 3, 2020
The agreement is for the investigational phase 1 gene therapy HMR59 that is given as a one-and-done shot into the eye to preserve vision in patients with geographic atrophy , which is a late-stage and severe form of age-related macular degeneration (AMD). An overactivity of complement damages cells in the macula in geographic atrophy.
Expert insights. Personalized for you.
117 
Let's personalize your content