Novartis’ $2 Million Gene Therapy Zolgensma Shows ‘Remarkable’ Results and Offers Hope for Children with SMA
XTalks
JUNE 8, 2021
With a price tag of over $2.5 In addition, two patients achieved a new milestone, “standing with assistance” without the use of the SMN2 -targeting oligonucleotide drug Spinraza (nusinersen, Ionis Pharmaceuticals). million, Zolgensma is currently the world’s most expensive drug. The study also found that early treatment was better.
110 
Let's personalize your content