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Novartis’ $2 Million Gene Therapy Zolgensma Shows ‘Remarkable’ Results and Offers Hope for Children with SMA

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With a price tag of over $2.5 In addition, two patients achieved a new milestone, “standing with assistance” without the use of the SMN2 -targeting oligonucleotide drug Spinraza (nusinersen, Ionis Pharmaceuticals). million, Zolgensma is currently the world’s most expensive drug. Why is Zolgensma So Expensive?