Remove tag dna-damage
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Lyfgenia and Casgevy Become First FDA-Approved Gene Therapies for Sickle Cell Disease

XTalks

The CRISPR system is dubbed to be molecular “scissors” that can cut out parts of genes that are abnormal, deactivating or replacing them with new strands of normal DNA. This has tremendous potential for curing diseases that are caused by faulty/mutated genes. The mutation causes red blood cells to develop a crescent or “sickle” shape.

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Unveiling Potential: Exploring Alpha Emitter Radiopharmaceuticals

XTalks

The aim of these compounds is to deliver radiation directly to the tumor cells, minimizing damage to surrounding healthy tissues. Alpha particles cause more localized and intense damage, reducing the risk of harm to adjacent healthy tissues.

DNA 66
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Roche’s quantitative COVID-19 antibody test; Janssen buys a gene therapy asset; Zimmer Acquires A&E Medical; Glaucoma research study: Merck chooses TriNKET cancer immunotherapy program; Ovid fails Angelman phase 3 study

Delveinsight

AMD Patients often have low levels of CD59, which is a protein that protects the retina from damage caused by a vital part of the body’s natural immune response called complement. An overactivity of complement damages cells in the macula in geographic atrophy. Merck chooses TriNKET cancer immunotherapy program.