Pharmaceutical Technology

JULY 14, 2022

Such movements have enabled pharmaceutical companies to increase their focus on rare diseases, and the number of orphan drug launches is steadily increasing. The choice of where to launch an orphan drug is an important and difficult decision. The choice of where to launch an orphan drug is an important and difficult decision.

Drugs 147

Drugs Medicine Marketing Development 147

pharmaphorum

APRIL 14, 2022

million price tag. The gene therapy has already been approved for marketing in the EU and UK, where it was launched at a cost of around $1.7 bluebird pulled it off the market last year however and retreated from the European market, saying the pricing and reimbursement environment was too hostile to make its business there viable.

Gene Therapy 64

Gene Therapy Gene Marketing Clinical Trials 64

pharmaphorum

AUGUST 18, 2022

The US approval comes three years after Zynteglo (betibeglogene autotemcel) was approved for the same indication in Europe, and subsequently withdrawn after bluebird concluded that it wasn’t possible to build a commercially viable business for the gene therapy as the pricing and reimbursement environment there was too “hostile.”

Gene Therapy 52

Gene Therapy FDA Approval Gene Clinical Trials 52

pharmaphorum

AUGUST 26, 2022

million for the one-shot therapy – in other words, after any discounts that it may offer or outcomes-based agreements – aiming to launch first in Germany followed by France. BioMarin has said Roctavian will be available at a ‘net’ price of around €1.5 million spread over five years. million spread over five years.

Gene Therapy 111

Gene Therapy Gene Antibody Marketing 111

XTalks

FEBRUARY 27, 2024

Despite high price tags of a couple of million dollars, gene therapy makers say they are working to ensure patients are able to access the treatments through patient assistance programs developed in conjunction with the support of governments. Sarepta hopes to clarify Elvidys’ effectiveness in older children in a confirmatory trial.

Research 59

Research Drugs Gene Therapy Clinical Trials 59

Cloudbyz

JUNE 1, 2023

Auto-launched Flows: These are flows that run in the background, requiring no user interaction. This is crucial in the modern business environment, where mobility and real-time access to data can provide a significant competitive edge. They can be embedded in a page, a button, a tab, or even a standalone URL.

Compliance 78

Compliance Development Branding Production 78

Pharmaceutical Technology

MARCH 17, 2023

On 16 March, Watt spoke at GlobalData webinar titled “Pharma [POLI]: Market Access Risk Outlook”, providing a current outlook on the pharmaceutical pricing and reimbursement environments around the world, including key reforms, risks and opportunities. GlobalData is the parent company of Pharmaceutical Technology.

Marketing 257

Marketing Drugs Research Analyst Manufacturing 257