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Gene Silencing Porphyria Treatment, Givlaari, Finally Wins Over England’s NICE Amid Stellar Long-Term Data

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The treatment came with an initial price tag of $39,000 per vial, which amounts to a total of $575,00 each year. Seizures occur due to the buildup of neurotoxins The condition can also cause other issues such as paralysis, insomnia and problems relating to the heart and lung. This leads to lowering of ALA and PBG levels.