Pharmaceutical Technology

SEPTEMBER 30, 2022

Spark Therapeutics’ Luxturna, indicated for inherited retinal disease (IRD), was the first gene therapy to be approved, in 2017, with a price tag of $850,000 for each eye. Gene therapies for rare inherited diseases are very expensive, as they tend to be the only therapeutic option available to patients and are often curative.

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Gene Therapy FDA Approval Gene Genetic Disease 289

Drug Discovery World

JANUARY 9, 2023

Using gene engineering, we are repurposing cancer cells to develop a therapeutic that kills tumour cells and stimulates the immune system to both destroy primary tumors and prevent cancer.” . The researchers also built a two-layered safety switch into the cancer cell, which can eradicate the therapeutic tumour cells if needed.

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Scientist Gene Editing Gene Engineer 52

XTalks

AUGUST 23, 2021

This is not a debate on approval,” said Stacie Weninger, PhD, president of the F-Prime Biomedical Research Initiative, in a focused topic session on the impact of drug approval on future clinical trials held on Tuesday July 27. With a $56,000 price tag for a year’s worth of treatment, Aduhelm is far from the most expensive drug on the market.

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Clinical Trials Clinical Trials Trials Drugs 52

XTalks

AUGUST 17, 2020

In this way, the platform allows for the generation of a vast number of therapeutic molecules from a very well formatted platform, which is the core strength of the technology. For their second molecule, the peptide was swapped out with a Wilm’s tumor 1 (WT1) peptide, and the third one has a KRAS peptide.

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Protein Engineer Immune Response In-Vivo 98

Drug Discovery World

NOVEMBER 13, 2023

Stefan Ewert, PhD, Associate Director, Biologics Center, Novartis Institutes for Biomedical Research, on: ‘Computational counterselection identifies nonspecific therapeutic biologic candidates’. The panel discussion will be hosted by chairperson Erasmus and Greiff on the current state of AI in antibody therapeutics.

Protein 59

Protein Antibody Engineer Scientist 59