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Risk adjusted net present value: What is the current valuation of Pharma Mar’s Ecubectedin?

Pharmaceutical Technology

The rNPV model is a more conservative valuation measure that accounts for the risk of a drug in clinical development failing to progress. Pharma Mar Overview Pharma Mar discovers, develops and markets marine-derived drugs to treat cancer. Its development pipeline includes PM14 for solid tumors, among others.

Hormones 100
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10 Key Learnings from Successful Cellular and Gene Therapy Trials for Rare Diseases

XTalks

Dr. Eagleton recently spoke on a webinar with his colleagues from Medpace about lessons learned from successful approaches from rare disease and gene therapy product approvals. The webinar included operational strategies for these trials from Laura Omoboni, MS, Executive Director of Clinical Trial Management.

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The biotech improving immunotherapies with AI

Drug Discovery World

Where cancers were previously understood by their tissue of origin and cell morphology, we can now define them based on their genotypes and molecular drivers. First, from the beginning, we designed the data production strategy with machine learning in mind and considered many factors that we knew were going to be important.

Genome 52
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FDA grants approval for bluebird’s Zynteglo to treat beta-thalassemia

Pharmaceutical Technology

The latest approval is based on findings from the Phase III clinical trials, HGB-207 (Northstar-2) and HGB-212 (Northstar-3), and the long-term follow-up LTF-303 study. 0 genotypes. The open-label, single-arm, 24-month Phase III trials enrolled 41 subjects of the age four to 34 years with non-?0/?0

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Global Roundup: Overland Pharma Launches in China to Provide Access to Breakthrough Therapies

The Pharma Data

The aim of the research will be to create a TGS IVD platform by optimizing a multi-layer approach encompassing the initial sample and library preparation, state-of-the-art sequencing technologies and improved genotyping procedures. To meet the increased demand, HALIX expands with two additional viral vector production, the company said.

In-Vivo 52
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Top 7 Pharma Industry Leaders in 2020 By the Numbers

Delveinsight

The company offers a variety of products under the three major business divisions i.e. Pharmaceutical, Medical Devices, and Consumer Health. Through its animal health division, it deals in Veterinary Pharmaceuticals and Vaccines (Livestock and Companion Animal Products). The annual sale of Merck and Company in the year 2020 was USD 47.9

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FDA Approves Oxlumo (lumasiran) for the Treatment of Primary Hyperoxaluria Type 1

The Pharma Data

The excess production of oxalate results in the deposition of calcium oxalate crystals in the kidneys and urinary tract and can lead to the formation of painful and recurrent kidney stones, nephrocalcinosis, progression to kidney failure, and systemic organ dysfunction. President of R&D at Alnylam.