Lipid nanoparticles and mRNA used to treat hereditary blindness
Drug Discovery World
JANUARY 17, 2023
They will lead research into using LNPs to deliver a gene editing tool that could delete bad genes in the photoreceptor cells and replace them with correctly functioning genes. . AAV has limited packaging capacity compared to LNPs and it can prompt an immune system response,” Sahay said.
Let's personalize your content