Pharmaceutical Technology

FEBRUARY 10, 2023

This is not the first treatment to come with a high price tag. Access to oncology medicines varies across countries, and their cost against safety/efficacy is generally perceived as being low, such as in the US. million, according to GlobalData’s Price Intelligence (POLI), making it the most expensive drug in the world.

Gene Therapy 263

Gene Therapy Marketing Gene Drugs 263

Rethinking Clinical Trials

OCTOBER 11, 2023

The Disparities Elimination through Coordinated Interventions to Prevent and Control Heart and Lung Disease Risk (DECIPHeR) initiative at the National Heart, Lung, and Blood Institute (NHLBI) is their first major effort to conduct implementation research. However, in an implementation trial, these are the most interesting measures.

Clinical Trials 152

Clinical Trials Clinical Trials Trials Research 152

XTalks

OCTOBER 26, 2021

After initial rejection from the National Institute for Health and Care Excellence (NICE) last year, the non-departmental public body of the Department of Health in England has now given the green light to the gene silencing treatment Givlaari (givosiran) for the treatment of the rare metabolic disorder, acute intermittent porphyria (AIP).

Gene Silencing 98

Gene Silencing Gene Clinical Trials Clinical Trials 98

pharmaphorum

JUNE 8, 2021

That was the damning conclusion of the influential Institute for Clinical and Economic Review (ICER) in the US to yesterday’s approval of Aduhelm (aducanumab), the first new treatment for Alzheimer’s since 2003, which it says has “no evidentiary basis.” billion in 2027.

Drugs 98

Drugs Marketing FDA Approval Trials 98

XTalks

FEBRUARY 27, 2024

Iovance Biotherapeutics’ Amtagvi (lifileucel) won US Food and Drug Administration (FDA) approval last week for the treatment of advanced melanoma, making it the first individualized tumor-infiltrating lymphocyte (TIL) therapy and the first T-cell therapy for a solid tumor to win US regulatory approval. Among responders, after 18.6

FDA Approval 52

FDA Approval Manufacturing In-Vivo Trials 52

XTalks

JUNE 8, 2021

With a price tag of over $2.5 It was first approved in the US in 2019 to treat children below the age of two with SMA. In England, five-month old baby Arthur became the country’s first SMA patient to receive the Zolgensma gene therapy last week through the National Health Service (NHS). Baby Arthur: First UK Patient.

Gene Therapy 110

Gene Therapy Gene Protein Trials 110

Rethinking Clinical Trials

FEBRUARY 22, 2023

The study is enrolling people where they are using social media, such as Facebook ads, twitter influencers, tv ads, interviews with print/electronic news outlets, national tv (an appearance on “The Talk” to discuss the study), targeted advertising, physicians, electronic health records.

Clinical Trials 130

Clinical Trials Clinical Trials Trials Nurses 130