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Vertex signs licence deal with CRISPR Therapeutics for diabetes therapies

Pharmaceutical Technology

The gene-editing technology allows for precise, directed changes to genomic DNA. It edits genes by precisely cutting DNA, then allowing natural DNA repair processes to take over. The system comprises the Cas9 enzyme and a guide RNA.

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Recon: Sanofi, GKS report positive interim results for COVID shot; Regeneron resumes lymphoma trials

The Pharma Data

At Illumina, the ‘era of the genome’ has arrived. Viatris Expects First “Interchangeable” Designation in July 2021 For Insulin Products ( Big Molecule Watch ). $DNA is once again on NYSE; FDA clears Soliris challenger for the market; Flagship’s thinking big again with eRNA; and more ( Endpoints ).

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The challenges and trends of cell & gene therapies 

Drug Discovery World

Research into genomic medicines is only at its infancy. CellTrans is currently awaiting an FDA decision for its cell therapy Lantidra, a treatment for patients with brittle type 1 diabetes mellitus whose symptoms cannot be well managed despite insulin therapy.