Remove Bacteria Remove Genetic Disease Remove Genetics Remove Research
article thumbnail

Gene Therapy and Pharmacokinetics

Camargo

The technology of gene therapy is possible due to extensive DNA research and our resulting understanding of many diseases on the genetic level, and it encompasses several mechanisms such as introducing new genes (gene addition) and inactivating or replacing mutated genes (gene editing). Formulation Considerations.

article thumbnail

Destiny Pharma granted award from Cystic Fibrosis Foundation  

Drug Discovery World

Destiny Pharma will establish a research project with the Cystic Fibrosis Foundation where it will establish the potential of its XF-73 drug as a treatment for MRSA infected cystic fibrosis patients. . Cystic fibrosis (CF) is a progressive, genetic disease that causes persistent lung infections and limits the ability to breathe.

Insiders

Sign Up for our Newsletter

This site is protected by reCAPTCHA and the Google Privacy Policy and Terms of Service apply.

article thumbnail

Education and empowerment would provide more equal access to care

pharmaphorum

Ella, 28, was diagnosed with cystic fibrosis – a rare genetic disease which causes a build-up of thick, sticky mucus in the lungs, digestive tract, and sinuses – at 18 months old. This sticky mucus gets trapped and breeds infections from bacteria I inhale,” says Ella, who adds she was “terrified” of doctors as a child.

Bacteria 102
article thumbnail

In a first, children with rare genetic diseases get mitochondrial transplants from their mothers

STAT News

At a far distant point in Earth’s ancient past, two separate, single-celled life forms — an archaeon and a bacteria — became one in an act either of symbiosis or enslavement, depending on which microbiologist you ask. These capsule-shaped organelles don’t just turn oxygen and nutrients into chemical energy.

article thumbnail

The future outlook for mRNA therapies

Drug Discovery World

Messenger RNA (mRNA) has come into focus within the drug discovery and development as an exciting tool to deliver genetic information. Whilst research into mRNA has been ongoing for decade, interest has sparked in recent years and research has begun to expand into areas of vaccinology, infectious diseases and other indications.

RNA 52
article thumbnail

Key Trends in the Life Sciences to Look Forward to in 2022

XTalks

percent, according to a report by BCC Research. In attempts to mask RNA from immune attack, researchers Drew Weissman and Katalin Karikó at the University of Pennsylvania switched out uridine, which is one of the four bases of the RNA code, for pseudouridine. billion by 2026 at a compound annual growth rate (CAGR) of 16.8