Drug Discovery World

NOVEMBER 7, 2022

Genomic healthcare data is critical to identify disease risk, ancestry, traits and response to medicines and aids in the development of new targeted therapies – precision medicines. WGS and Dante’s genomic reports will provide information about predisposition to genetic diseases, genetic carrier information and more.

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Genome Genomics Development Genetics 98

Drug Discovery World

MARCH 21, 2023

Published in Molecular Cell, the study explains the rules determining to what extent genes respond to CRISPR activation, ensuring that future research can be designed as efficiently as possible. CRISPR activation (CRISPRa) is a type of CRISPR gene editing that is used to overexpress certain genes.

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Research Gene Gene Editing Genome 52

Pharmaceutical Technology

JANUARY 10, 2023

Asklepios BioPharmaceutical has entered a research partnership and option agreement with ReCode Therapeutics for exploring its single-vector gene-editing platform. The new solution will enable complete gene insertion by delivering the gene-editing tool and DNA as mixed cargo to desired targets in one LNP.

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Gene Editing Gene Gene Therapy Genetics 130

pharmaphorum

FEBRUARY 17, 2022

Oxbryta is the first medicine approved in Europe that directly prevents sickle haemoglobin (HbS) polymerisation, the molecular basis of sickling and destruction of red blood cells in SCD, and has been tipped to become a $1 billion-plus blockbuster at peak.

Drugs 59

Drugs Gene Therapy Gene Editing Gene 59

The Pharma Data

DECEMBER 13, 2020

“Our company and R&D portfolio are entering into an exciting phase, as evidenced by the recent close of Series B financing and submission of the first gene editing product IND in China,” said Dong Wei, Ph.D.?CEO

Business Development 40

Business Development Development Gene Editing In-Vivo 40

XTalks

DECEMBER 29, 2022

In 2023, a number of gene therapies are expected to get the FDA green light. This includes the first ever CRISPR gene editing therapy from Vertex and CRISPR therapeutics for sickle cell disease (SCD) and transfusion-dependent beta thalassemia (TDT).

Life Science 52

Life Science Gene Therapy Gene Manufacturing 52

Scienmag

APRIL 21, 2021

New approach to gene therapy can correct any disease-causing mutation within a gene UNIVERSITY PARK, Pa.

Gene 52

Gene Gene Editing Gene Therapy Genetic Disease 52

pharmaphorum

JANUARY 10, 2022

The company has also stated, at the same time as the study was announced, that it will look at developing mRNA technology in oncology and genetic diseases. Similar to Pfizer, Sanofi noted that bringing the companies into its portfolio would allow it to leverage research capabilities in oncology and inflammatory disease.

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XTalks

DECEMBER 22, 2021

RNA therapeutics hold promise as powerful treatments for diseases, including those that are genetic-based. The gene-editing tool CRISPR edits DNA using specialized strands of guide RNA and endogenous cellular mechanisms of RNA interference. RNA Therapeutics. The deal is worth $1.5

Life Science 98

Life Science RNA Vaccination Vaccine 98

Drug Discovery World

FEBRUARY 22, 2024

With the breadth and range of central nervous system disorders – for example Parkinson’s disease and multiple sclerosis – facing the global population there is an unmet need within this area of drug discovery. We should not overlook neuropsychiatric conditions such as depression, anxiety and addiction either.

Drugs 57

Drugs Gene Clinical Trials Clinical Trials 57