Gene Therapy and Nurses - Clinical Research Informer

?5 Things You Need to Know from Our Recent Gene Therapy Webinar

Worldwide Clinical Trials

JUNE 15, 2022

At the end of May, we hosted a webinar titled “ Changing Times, Changing Therapies: Keeping Up with Advancements in Cell and Gene Therapies ” to provide a quick update on the latest advancements and ongoing in development of these advanced therapeutics. Around 40% of clinical holds are for gene therapy programs.

Gene Therapy

Gene Therapy Gene Clinical Trials Clinical Trials

Vyjuvek Gets FDA Nod as First Topical Gene Therapy for Rare Skin Disease

XTalks

MAY 26, 2023

Krystal Biotech’s Vyjuvek has been awarded US Food and Drug Administration (FDA) approval to make it the first topical gene therapy for the treatment of wounds in patients with the rare, often debilitating skin disease dystrophic epidermolysis bullosa (DEB). As a topical treatment, it is also the first readily redosable gene therapy.

Gene Therapy

Gene Therapy Gene FDA Approval Dermatology

Clinical Research Nurse Finds Opportunities via LinkedIn: We Discuss Gene Therapy, Career Growth!

Clinical Trial Gurus

AUGUST 26, 2021

Clinical research nurses have the background and the experience to virtually demand a great amount of interest from prospective employers. In this video I interview Michele Blue, a research nurse from an academic medical center (AMC). We discuss her career, job prospects, and a lot of other topics related to clinical research.

Nurses

Nurses Clinical Research Gene Therapy Research

STAT+: A young boy’s nightmare diagnosis, and the $3 million one-time treatment that will likely save his life

STAT News

APRIL 3, 2023

When the long-awaited moment arrived, a nurse helped Adam Hess loosen a tiny plastic clamp on an intravenous line leading to the chest of his son, who lay asleep in a bed at Boston Children’s Hospital. They had been modified in a lab by adding a functional gene to compensate for a defective one.

Gene Therapy

Gene Therapy Nurses Gene Doctors

Novartis hails digital strategy as profits hold up during pandemic

pharmaphorum

JANUARY 26, 2021

In China, Novartis has been working with the internet multinational Tencent on an AI-enabled “digital nurse” to manage heart disease. Sales of spinal muscular atrophy gene therapy Zolgensma have been hit because it requires a course of drugs to suppress the immune system before prescription.

Doctors

Doctors Doctor Sales Clinical Trials

The Benefits of Working for a Rapidly Growing Global Clinical Research Organization (CRO) like Medpace

XTalks

OCTOBER 18, 2022

Cellular and gene therapy. Radiation therapy. Medpace has various opportunities for nurses and other healthcare professionals. Hematology and oncology. Infectious diseases and vaccines. NASH and liver disease. Neurology and psychiatry. Nephrology. Ophthalmology. Pediatrics. Rare diseases.

Clinical Research

Clinical Research Research Clinical Trials Clinical Trials

Could virtual reality become an essential tool for healthcare education?

pharmaphorum

JUNE 1, 2022

According to the World Health Organization, the world will need more than 40 million new doctors, nurses, frontline healthcare workers, and various other healthcare professionals by 2030. Spark Therapeutics developed a VR product , alongside a partner, to teach haemophilia patients about gene therapy. The training challenge.

Vaccination

Vaccination Vaccine Doctors Doctor

Vertex and CRISPR Therapeutics submit BLAs to FDA for exa-cel

Pharmaceutical Technology

APRIL 4, 2023

We want to thank the clinical trial participants and the sickle cell and beta thalassemia communities, as well as the physicians, nurses, coordinators, caregivers and friends who support them.” Cell & Gene Therapy coverage on Pharmaceutical Technology is supported by Cytiva.

Gene Therapy

Gene Therapy Gene Editing In-Vivo Gene

How the US’s pending PIE Act will improve patient access to medication

pharmaphorum

JUNE 27, 2022

” AMCP’s members include pharmacists, nurses, and clinicians with varying expertise in clinical trial processes and data. With the three-year delay, the fear and concern are that the wait will only grow with new types of treatments being explored, such as cell and gene therapies, where little data already exists.

FDA Approval

FDA Approval Manufacturing Clinical Trials Clinical Trials

Strategies to Successfully Manage Complex Cell Therapy Clinical Trials

XTalks

FEBRUARY 10, 2023

“At Medpace, we go further by having a specialist regulatory technical team support our clinical trials, particularly for cell-therapy studies.” Medpace has IP experience with both autologous and allogeneic cellular products, ex vivo and in vivo gene transfer, and a number of different gene-editing mechanisms. If so, why?

Clinical Trials

Clinical Trials Clinical Trials Trials Gene Therapy

Digital health: the new normal?

pharmaphorum

DECEMBER 2, 2021

The aims of Babylon’s app go further than to provide an easy-access doctor and include leveraging patient data to provide doctors and nurses with user-inputted information to inform decision-making processes. Tapping into data. Personalised medicines have become an established part of treatment programs, especially when treating cancer.

Genetics

Genetics Doctors Doctor Pharmacy

Three pillars of post-pandemic launch excellence

pharmaphorum

APRIL 16, 2021

Because we knew that Orphan Medicines, led by the gene therapy Zolgensma and the Cystic Fibrosis treatment Trikafta, had in many cases actually outperformed expectations in 2020, we assessed the first six months of sales for New Active Substance launches with and without Orphan medicines.

Sales

Sales Marketing Medicine Doctors

Considerations for Neuroscience Trials with Intrathecal Delivery and Other Methods of Direct CNS Administration

XTalks

AUGUST 30, 2022

We know that a lot of different pathologies, especially as we’ve entered the era of molecular medicine and gene therapies, cause many of the same symptoms and work through final common pathways. However, a drawback is that the dose and neuronal specificity of gene therapy is still poorly understood even in translational models.

Trials

Trials Drug Delivery Drugs Gene

CheckMate -577, a Phase 3 Trial Evaluating Opdivo (nivolumab) as Adjuvant Therapy for Patients with Resected Esophageal or Gastroesophageal Junction Cancer, Meets Primary Endpoint of Disease-Free Survival

The Pharma Data

AUGUST 11, 2020

In the field of immune cell therapy, this includes registrational CAR T cell agents for numerous diseases, and a growing early-stage pipeline that expands cell and gene therapy targets, and technologies. It is not known whether OPDIVO or YERVOY is present in human milk. Serious Adverse Reactions.

Trials

Trials Hormones Clinical Trials Clinical Trials

CheckMate -649, a Phase 3 Trial Evaluating Opdivo (nivolumab) Plus Chemotherapy vs. Chemotherapy, Meets Primary Endpoints Demonstrating Superior Overall Survival and Progression-Free Survival in First-Line Treatment of Gastric and Esophageal Cancers

The Pharma Data

AUGUST 11, 2020

In the field of immune cell therapy, this includes registrational CAR T cell agents for numerous diseases, and a growing early-stage pipeline that expands cell and gene therapy targets, and technologies. It is not known whether OPDIVO or YERVOY is present in human milk. Serious Adverse Reactions.

Trials

Trials Hormones Clinical Trials Clinical Trials

Clinical Research Informer

?5 Things You Need to Know from Our Recent Gene Therapy Webinar

Vyjuvek Gets FDA Nod as First Topical Gene Therapy for Rare Skin Disease

Trending Sources

Clinical Research Nurse Finds Opportunities via LinkedIn: We Discuss Gene Therapy, Career Growth!

STAT+: A young boy’s nightmare diagnosis, and the $3 million one-time treatment that will likely save his life

Novartis hails digital strategy as profits hold up during pandemic

The Benefits of Working for a Rapidly Growing Global Clinical Research Organization (CRO) like Medpace

Could virtual reality become an essential tool for healthcare education?

Vertex and CRISPR Therapeutics submit BLAs to FDA for exa-cel

How the US’s pending PIE Act will improve patient access to medication

Strategies to Successfully Manage Complex Cell Therapy Clinical Trials

Digital health: the new normal?

Three pillars of post-pandemic launch excellence

Considerations for Neuroscience Trials with Intrathecal Delivery and Other Methods of Direct CNS Administration

CheckMate -577, a Phase 3 Trial Evaluating Opdivo (nivolumab) as Adjuvant Therapy for Patients with Resected Esophageal or Gastroesophageal Junction Cancer, Meets Primary Endpoint of Disease-Free Survival

CheckMate -649, a Phase 3 Trial Evaluating Opdivo (nivolumab) Plus Chemotherapy vs. Chemotherapy, Meets Primary Endpoints Demonstrating Superior Overall Survival and Progression-Free Survival in First-Line Treatment of Gastric and Esophageal Cancers

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