Drug Discovery World

FEBRUARY 8, 2024

Regulatory agencies consider genotypic identification to be more reliable than phenotypic methods. Per regulatory guidelines, the implementation of an environmental monitoring programme is required to comply with good manufacturing practices and identification of microorganisms to species level is a minimal requirement.

Manufacturing 52

Manufacturing Genotype Gene Therapy Compliance 52

Drug Discovery World

FEBRUARY 1, 2024

Regulatory agencies consider genotypic identification to be more reliable than phenotypic methods. Per regulatory guidelines, the implementation of an environmental monitoring programme is required to comply with good manufacturing practices and identification of microorganisms to species level is a minimal requirement.

Manufacturing 52

Manufacturing Genotype Gene Therapy Compliance 52

Pharmaceutical Technology

DECEMBER 15, 2022

Therefore, there is also a significant need for new therapies that target the underlying cause of CFD that may offer a cure for patients living with severe disease, or for patients with genotypes such as dysfibrinogenemia and hypodysfibrinogenemia, who are often ineligible for treatment with HFCs.

Marketing 130

Marketing Production Genotype Development 130

Drug Discovery World

FEBRUARY 9, 2024

DDW recently hosted a webinar ‘Discover how iPSC derived cells can be used to support the development of drug and gene therapies’, supported by DefiniGEN. In addition, stable cell lines derived from cancers represent a single and karyotypically abnormal genotype. Are there any ethical boundaries behind the use of iPSCs?

Gene Therapy 52

Gene Therapy Gene Development Drugs 52

Drug Discovery World

SEPTEMBER 19, 2023

In addition, stable cell lines derived from cancers represent a single and karyotypically abnormal genotype. ‘ Discover how iPSC derived cells can be used to support the development of drug and gene therapies’ will take place on 28 September 4PM BST, 5PM CEST, EDT 11AM, PDT 8AM. Register for free here.

Gene Therapy 52

Gene Therapy Gene Development Protein 52

Drug Discovery World

SEPTEMBER 12, 2023

In addition, stable cell lines derived from cancers represent a single and karyotypically abnormal genotype. ‘ Discover how iPSC derived cells can be used to support the development of drug and gene therapies’ will take place on 28 September 4PM BST, 5PM CEST, EDT 11AM, PDT 8AM. Register for free here.

Gene Therapy 52

Gene Therapy Gene Development Drugs 52

pharmaphorum

JANUARY 24, 2023

Pharma has used this to begin creating targeted treatments, such as gene therapies , which are able to hone in on gene mutations that cause health issues and eradicate or replace the faulty gene. Scientists are able to study the aggregated, de-identified genetics of these individuals.

Genetics 92

Genetics Drugs Genome Project Biobanking 92

Pharmaceutical Technology

AUGUST 18, 2022

A custom-made, one-dose gene therapy, Zynteglo is indicated for such patients who need red blood cells (RBCs) transfusions on a regular basis. 0 genotypes. A genetic blood ailment, beta-thalassemia is caused by beta-globin gene mutations and results in a substantial decline or lack of production of adult haemoglobin.

Gene Therapy 246

Gene Therapy Gene Genotype Genetics 246

pharmaphorum

DECEMBER 9, 2020

bluebird bio has presented long-term data from its Zinteglo one-time gene therapy for the blood disorder beta-thalassaemia, as the company continues talks with payers in Europe to bring the ultra-pricey treatment to market. The post Bluebird trumpets long-term data from beta-thalassaemia gene therapy appeared first on.

Gene Therapy 53

Gene Therapy Gene Genotype Marketing 53

Drug Discovery World

AUGUST 25, 2023

Also, stable cell lines derived from cancers represent a single and karyotypically abnormal genotype. Hepatocellular carcinoma-derived cell lines, such as HepG2s, are less proliferative than CHO or HEK cells but remain readily expandable and retain aspects of hepatocyte function.

Gene Therapy 52

Gene Therapy Gene Development Genotype 52

The Pharma Data

DECEMBER 9, 2020

The Chinese biopharmaceutical industry is growing in leaps and bounds, but there is still a huge unmet need when it comes to getting patients access to the breakthrough therapeutic modalities and platforms like RNAi, cell and gene therapy and others. A solution could be at hand with Overland Pharmaceuticals.

In-Vivo 52

In-Vivo In-Vitro Antibody Development 52

Drug Discovery World

SEPTEMBER 5, 2023

In addition, stable cell lines derived from cancers represent a single and karyotypically abnormal genotype. ‘ Discover how iPSC derived cells can be used to support the development of drug and gene therapies’ will take place on 28 September 4PM BST, 5PM CEST, EDT 11AM, PDT 8AM. Register for free here.

Development 59

Development Drugs Protein Genotype 59

Drug Discovery World

SEPTEMBER 26, 2023

In addition, stable cell lines derived from cancers represent a single and karyotypically abnormal genotype. ‘ Discover how iPSC derived cells can be used to support the development of drug and gene therapies’ will take place on 28 September 4PM BST, 5PM CEST, EDT 11AM, PDT 8AM. Register for free here.

Development 52

Development Drugs Protein Genotype 52