Remove tag next-generation-sequencing
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First gene therapy trial for Hunter syndrome opens in Manchester, UK

Drug Discovery World

Next generation stem cell gene therapy Children with Hunter syndrome have a missing gene, meaning they cannot produce an important enzyme called iduronate-2-sulfatase or IDS. Professor Bigger said: “This is a next generation stem cell gene therapy approach, which allows transit of the IDS enzyme into the brain.

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AI-Powered Precision Engagement in Commercial and Medical Functions

Intouch Solutions

With today’s current possibilities, there is still so much more on the horizon for precision engagement, especially when combining it with the new and revolutionary Generative Pre-trained Transformers Artificial Intelligence (GPT AI). Generating “data-driven” editorial plans. So, what is precision engagement?

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What to expect from PEGS Europe 2023: Day 3

Drug Discovery World

On Day 3, Thursday 16 November 2023, the tracks include: the second part of machine learning for protein engineering, antibodies against membrane protein targets, engineering bispecific antibodies, next-generation immunotherapies, protein stability and formulation, and protein process development.

Protein 57
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Spatial Genomics, Transcriptomics and Proteomics Solutions – An Amelioration of Tissue Analytics

Roots Analysis

Recent advances in multi-omics approaches, including genomics, transcriptomics, proteomics, metabolomics, cytometry and imaging, in combination with bioinformatics and biostatistics, have been translated into several popular bioanalytical platforms, such as next-generation sequencing (NGS), single-cell analysis, flow cytometry and mass spectrometry.

Genome 52
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What to expect from PEGS Europe 2023: Day 2

Drug Discovery World

The two luncheon presentations include: Maurice Brozzo, Global Antibody Specialist, Charles River, on: ‘The antibody discovery journey: from next-generation libraries to efficacy and safety’. The panel discussion asks what the next game changer will be in the CAR T cell field. Filip Borgions, Ph.D,

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Women in Science Who Have Paved the Way Forward in Genetics

XTalks

The Human Genome Project recently marked 20 years since the publication of the first full sets of human genomic sequences, an endeavor that spanned well over a decade. Today, new next-generation sequencing technologies allow for the sequencing of complex genomes within just a day or two. Emmanuelle Charpentier.

Genetics 119