pharmaphorum

AUGUST 8, 2022

The GBT deal comes at a time when the market for SCD therapies is undergoing significant change, with multiple new drugs reaching the market after years of stagnation and progress also being made with genetic therapies from the likes of bluebird bio, Vertex Pharma/CRISPR Therapeutics and Precision Bio/Novartis.

Marketing 111

Marketing Sales Gene Editing Antibody 111

Pharmaceutical Technology

DECEMBER 22, 2022

The funding will offer capital to extend Blueprint’s varied pipeline toward marketing as well as to continue seeking strategic and synergistic business development prospects. This genetic-led approach will also aid in expediting the approval of new treatments. Innovation.

Insulin 130

Insulin Production Development Genetics 130

pharmaphorum

SEPTEMBER 21, 2021

In other cases, rare CNS conditions may be passed on from one generation to the next without knowledge or understanding that the reason for suffering or death among previous generations was genetic in basis and therefore identifiable, and perhaps even treatable.

Gene Therapy 90

Gene Therapy Gene Clinical Trials Clinical Trials 90

XTalks

MAY 17, 2024

Prior to joining Calliditas Therapeutics as CMO, he held roles at GlaxoSmithKline (GSK) and Takeda, focusing on clinical and business development in rare diseases. I’ve had a great passion for drug development in rare diseases,” says Dr. Philipson, underscoring a commitment that would shape his career’s trajectory.

Development 52

Development Drugs Clinical Trials Clinical Trials 52

Pharmaceutical Technology

JULY 14, 2022

It is estimated that there are currently more than 7,000 orphan diseases, many of which are considered life-threatening and most of which have a genetic basis. Despite this high number, orphan diseases are rare by definition, affecting around one in 2,000 people as defined by the European Union.

Drugs 147

Drugs Medicine Marketing Development 147

Pharmaceutical Technology

JUNE 19, 2023

Pharmaceutical companies are putting their trust in the immense potential this new generation of medicine has for treating individuals with rare genetic diseases, which currently affect an estimated 280 million patients worldwide. Cell and gene therapies are not your typical clinical supply chain.

Gene Therapy 130

Gene Therapy Gene Packaging Packaging 130

The Pharma Data

NOVEMBER 3, 2020

Nasdaq:LOGC) (LogicBio), a company dedicated to extending the reach of genetic medicine with pioneering targeted delivery platforms, announced today the U.S. LogicBio Therapeutics is dedicated to extending the reach of genetic medicine with pioneering targeted delivery platforms. LEXINGTON, Mass., About LogicBio Therapeutics.

Clinical Trials 52

Clinical Trials Clinical Trials Gene Editing Genomics 52

The Pharma Data

DECEMBER 17, 2020

Most recently, Cadavid served as senior vice president and Head of Clinical Development at Fulcrum Therapeutics where he led the development of multiple small molecules for the treatment of genetically defined rare diseases. She joined VMS BioMarketing in 2008 and has served as its president and CEO since 2011.

Development 52

Development Gene Therapy Engineer Life Science 52

The Pharma Data

DECEMBER 8, 2020

Now poised to advance a robust therapeutics pipeline to clinical development, Nuance will use the funds for ongoing R&D of existing products and business development of potential new assets. Through its Shielded Living Therapeutics platform, the company is developing functional cures for chronic diseases.

RNA 52

RNA Antibody Life Science Protein 52

The Pharma Data

NOVEMBER 10, 2020

AlzeCure aims to pursue its own projects through preclinical research and development to an early clinical phase and is continuously working with business development to find suitable out-licensing solutions with other pharmaceutical companies. The main risk factors to develop Alzheimer’s are age and genetic causes.

Development 40

Development Drugs Protein Research 40

The Pharma Data

NOVEMBER 5, 2020

Corporate and Business Development Update. The Company’s 2020 financial guidance does not assume the completion of any significant business development transactions not completed as of the date of this press release. (4). government.

Sales 52

Sales Production Manufacturing Antibody 52

pharmaphorum

DECEMBER 14, 2022

Mitochondrial dysfunctions cause more than 50 diseases, including Alzheimer’s and Parkinson’s diseases and rare genetic disorders. Paolo is a life sciences executive with over 20 years of experience in venture capital, R&D, external innovation, and business development. Supporting efforts to address mitochondrial diseases.

Life Science 105

Life Science Development Business Development Genetics 105

The Pharma Data

OCTOBER 15, 2020

The committee is tasked with supporting BeyondSpring’s business development activities related to its lead asset, Plinabulin, and other pipeline assets. Mukul Agarwal, former vice president of Corporate Development, at Forty Seven, Inc., BeyondSpring – BeyondSpring Inc. Sabbagh will replace David Thompson who is retiring.

In-Vivo 52

In-Vivo Business Development Manufacturing Development 52

The Pharma Data

OCTOBER 26, 2020

The FDA has granted V181, the company’s investigational dengue vaccine in Phase 1 development, Fast Track designation. Business Developments. formerly known as Seattle Genetics, Inc.) Merck and Seagen Inc.

Sales 40

Sales Vaccination Vaccine Production 40

XTalks

OCTOBER 1, 2020

Dr. Lin has made several transitions throughout her career, from being a clinician at an academic center, to academic research, to heading business development in industry. Working on finding therapies for genetic diseases at NeuBase, Dr. Sooter says, “Everyday, we get up and that’s our goal and it really drives everyone.

Scientist 52

Scientist In-Vitro Research Life Science 52

Pharmaceutical Technology

MARCH 20, 2023

In APAC, for example, industry commentators are predicting that the pharmaceutical sector’s historic focus on genetics and manufacturing will shift towards cutting-edge technology. Against this backdrop, new specialisations are cropping up in regional investment activity and cash raising techniques. Source: GlobalData.

Gene Therapy 225

Gene Therapy Genome Genomics Gene 225

Pharmaceutical Technology

MARCH 20, 2023

It’s home to the highest genetic diversity of humans on the planet and it’s filled with potential participants who are more and more urbanised and eager to be part of the clinical trials.” However, Africa currently accounts for a very low percentage of global clinical trials, with estimates putting it at approximately 2.5%. “You

Clinical Trials 130

Clinical Trials Clinical Trials Trials Clinical Supply Chain 130

Pharmaceutical Technology

MAY 9, 2023

Jamaels recently brought together members of the business development team and new starters face-to-face for the first time to brainstorm how to remain competitive and price smarter. “When you have teams talking to each other and understanding each other’s requirements, then you can improve processes and raise the quality of the work.”

Clinical Trials 130

Clinical Trials Clinical Trials Trials Big Data 130