FDA Approves First Drug to Improve Growth in Children with Most Common Form of Dwarfism
The Pharma Data
NOVEMBER 21, 2021
People with achondroplasia have a genetic mutation that causes a certain growth regulation gene called fibroblast growth factor receptor 3 to be overly active, which prevents normal bone growth. The most common side effects of Voxzogo include injection site reactions, vomiting and decreased blood pressure. Inheritance is autosomal dominant.[1][2]
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