Drug Discovery World

JANUARY 25, 2024

Japan-based pharma company Kyowa Kirin has successfully completed the acquisition of gene therapy developer Orchard Therapeutics. Libmeldy is approved by the European Commission (EC) and UK Medicines and Healthcare products Regulatory Agency (MHRA).

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XTalks

OCTOBER 4, 2023

This evidence is indispensable in garnering support from healthcare stakeholders and payers who must evaluate whether products offer value for money within constrained healthcare budgets. What types of product portfolios do you oversee now and have overlooked previously?

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pharmaphorum

NOVEMBER 30, 2020

Cure Rare Disease’s Rich Horgan discusses the importance of preclinical NAbs screening and helping rare disease patients better understand their eligibility for gene therapies. This is particularly pertinent in rare diseases, as a number of gene therapy products use viral delivery methods to deliver the transgene to target organs.

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Pharmaceutical Technology

MAY 26, 2023

Pharma company merger and acquisition (M&A) activity in the first half of 2023 has remained relatively low, consistent with the second half of last year, but investors predict deals will increase later in 2023. Experts at PWC, Goldman Sachs, and Morgan Stanley agree that pharma-related M&A is expected to pick up in 2023.

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pharmaphorum

SEPTEMBER 29, 2020

As of 2018, there were over 1,100 cancer therapies in development, and as of 2020, 362 of them were cell and gene therapies. These benefits strengthen capabilities and accelerate product development, ultimately producing higher quality and more effective therapies.

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Drug Discovery World

AUGUST 4, 2023

With so many exciting novel treatments emerging from the labs, biotechs and pharma companies need to understand the potential unknowns as well as the known considerations if they are to optimise their impact in the real world. Other challenges involve talent gaps, particularly now that cell and gene therapy manufacturing is maturing.

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pharmaphorum

DECEMBER 29, 2022

A new study by AspenTech in collaboration with FT Longitude confirms, for example, how digital transformation is on the rise in pharma to meet the demands of such new modalities as cell and gene therapies, and biologics. Crisis readiness and digital workflows. Removing manual pen-on-paper processes should be an obvious first step.

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Drug Discovery World

MAY 6, 2024

A more established Amsterdam-based enterprise is gene therapy company uniQure, developer of etranacogene dezaparvovec, the first gene therapy for haemophilia B, which was approved for use in the US in November 2022 and in the EU in February 2023. The government and organisations here are so positive and enthusiastic.

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XTalks

OCTOBER 22, 2020

In this sense, pharmaceutical companies have developed different strategies to produce a wide variety of advanced therapy medicinal products (ATMP) and biological products, such as monoclonal antibodies, recombinant proteins, gene therapy viral vectors, CAR-T cells and oncolytic viruses, in order to deliver new medical needs in our society.

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pharmaphorum

MARCH 22, 2022

The pharma industry’s overall push into industry 4.0 for manufacturing, with the aim of streamlining and enabling greater automation through adoption of digital tools, is leading to greater interest in the potential for VR and AR to improve efficiency and reduce costs in production. The importance of manufacturing.

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pharmaphorum

NOVEMBER 30, 2022

The biggest gathering of pharma companies in Europe right now on the commercial side, the Veeva Systems Summit permits the sharing of best practices and of new ideas. How can it fund the necessary production of medicine? As Crooks said, data is data, but companies have to constantly try to transfer that into actual knowledge.

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Drug Discovery World

OCTOBER 4, 2022

This year’s event will cover some of the most exciting advancements in areas spanning screening, automation, high content imaging, disease models, cell and gene therapies and how innovation is being driven through partnerships and collaborations. Cell and gene therapies. In 2021, levels of investment hit an all-time high at $22.7

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Drug Channels

FEBRUARY 6, 2024

PAP – Patient Assistance & Access Programs Download Agenda | See Who’s Speaking The experts will be taking the most pressing challenges industry is facing head on, including: Emerging Policy Changes and Enforcement Actions The Impact of AFPs on PAPs Program Automation for Operational Efficiency Ensuring Health Equity Where It Matters Most Patient (..)

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XTalks

DECEMBER 29, 2022

For example, on the pharma and biotech side, there has been growing demand for new drugs and biologics, from new classes of dual-action diabetes and weight loss drugs like Ozempic and Mounjaro to life-saving gene therapies. 1. Cell and Gene Therapies. Here are four life sciences trends to look out for in 2023.

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pharmaphorum

NOVEMBER 22, 2022

Francis, who is currently CEO of gene therapy specialist Purespring Therapeutics and cardiovascular drug developer company Forcefield Therapeutics, is due to take the top job at Teva on 1 January, and will serve as the pharma company’s president. Richard Francis.

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Camargo

MARCH 9, 2021

The FDA revealed that pharma companies are not forthcoming when they publicly disclose the reasons behind a refuse-to-file (RTF) letter from the Agency. In fact, when they do disclose their existence, companies disclosed only 5% of the reasons for the RTF. in 2020) Keytruda. FDA Inspection Delays During the Pandemic, Continued.

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The Pharma Data

JANUARY 24, 2021

.–( BUSINESS WIRE )– Faze Medicines , a biotechnology company pioneering therapeutics based on the groundbreaking new science of biomolecular condensates, today announced that it has appointed Philip Vickers, Ph.D., Preclinical and clinical programs at Northern Biologics were acquired by big pharma companies in 2020.

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Drug Discovery World

OCTOBER 16, 2023

Dr Salako says there are some clear fields of work associated with different areas, which include: Hertfordshire as a cell and gene therapy hub, with a number of companies in this space clustered around Stevenage. Cambridge is a focal point for many pharmaceutical companies working in this therapeutic area.

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pharmaphorum

APRIL 26, 2022

Research into the area is being made possible through advancements in technology, such as being able to sequence genes at scale, allowing researchers to gain more detailed genetic data on the microbiome. In the trial, Seres announced that the product candidate had met its primary endpoint, showing a statistically significant 30.2%

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pharmaphorum

APRIL 28, 2022

Despite the inherent difficulties, major pharma companies do take aim at rare diseases, usually with dedicated units focusing on clusters of rare diseases that afflict the same part of the body. How big pharma tackles rare diseases. It’s a different business model, if you will,” Miquel said. “So So that is the trick.

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XTalks

DECEMBER 20, 2023

‘No Time to Wait’ Ad Campaign from BMS-Pfizer Features Basketball Legend Kareem Abdul-Jabbar for AFib Awareness As pharma TV advertising remained popular in 2023, so did partnerships between pharma companies and celebrities for disease and drug campaigns.

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Drug Discovery World

MARCH 29, 2023

The commission is looking to put more pressure on pharma companies to report such shortages, and to offer a drug’s marketing authorisation to another company before withdrawing it from the market. This looks like it may change shape in the future for the region, if the proposal put forward by the commission is adopted.

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Pharmaceutical Technology

MAY 24, 2023

By Luisa Sterkel & Joana Loureiro , Tenthpin Consultants The promise and potential of cell and gene therapies (CGT) has emerged in the recent past and currently over 1.500 CGT are registered for clinical trials holding great hope for the treatment of challenging and uncurable diseases.

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pharmaphorum

SEPTEMBER 11, 2019

The advent of highly novel cell and gene therapies as well as prescription digital therapeutics is providing a serious set of forces for change in the market. Another comes from the challenges developed markets face, which renews the urgency for pharma companies to spread their launch successes beyond traditionally core markets.

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pharmaphorum

NOVEMBER 16, 2020

During his tenure the EMA also implemented new rules to encourage the development of advanced therapy medicinal products (ATMPs) like gene and cell therapies, and the introduction of the PRIME fast-track review for promising medicines. Emer Cooke.

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Delveinsight

AUGUST 6, 2020

Hereditary ATTR amyloidosis , also known as Familial ATTR, is an autosomal dominant disease and a result of mutations in the TTR gene, thus it is passed down from one generation to the next one. They help in preventing confrontational changes and dissociation of protein, and not halt the production of the protein.

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Pharmaceutical Technology

JUNE 14, 2023

Future waves of approvals for ATMPs (advanced therapy medicinal products, e.g., cell and gene therapies) will heighten demand on the contract packaging industry, further increasing the need for advanced cold chain solutions and specialized packaging designed to withstand cryogenic temperatures.

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Drug Discovery World

FEBRUARY 10, 2023

A good part of half of those are within pharma. The pharma companies that are based in Sweden, are international ones, and often have a marketing and commercial side but maybe not that drug development side that really brings that key focus area between the development and commercialisation.” It’s also a seal of quality.

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pharmaphorum

DECEMBER 23, 2020

The results also suggest further uses for the drug in early disease and more revenues to come from one of the company’s biggest success stories from the last decade. Biogen and Denali will co-market the lead LRRK2 product in the US and China, and Biogen will commercialise in all other markets. Rare disease progress.

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Pharmaceutical Technology

SEPTEMBER 8, 2022

The information contained within the download document is designed for pharmaceutical executives, developers, research scientists and associates, regulatory solutions consultants, and any other individual involved in API biologics production in the pharmaceutical industry.

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XTalks

APRIL 16, 2024

Nurtec ODT, a product of Biohaven Pharmaceuticals, is an oral tablet designed for the acute and preventive treatment of migraine in adults. The same criticism erupted on Gaga’s recent Instagram posts about her new ad with Pfizer, with some people lambasting her for getting paid by the company.

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Pharmaceutical Technology

FEBRUARY 13, 2023

Several biotech companies and researchers are now exploring medical devices and gene therapies to address not just common forms of epilepsy, but also rare conditions such as Dravet Syndrome. Meanwhile, others are researching the link between gene variation and different responses to treatments.

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pharmaphorum

NOVEMBER 23, 2022

We have built a product that is universal, that can really bring any pharma party, any payers in any market to really work together. We wanted to bring a product to market that is already at scale and futuristic, to allow them to scale quick. [So,] So,] that really resonated – patient centricity.

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Drug Discovery World

SEPTEMBER 28, 2022

Its application in pharma, most commonly in drug discovery, has been steadily growing with global partnerships between tech vendors and pharma companies becoming more commonplace. Biotech and AI companies founded by purely tech professionals often opt to bring in pharma executives with insider knowledge further down the line.

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The Pharma Data

OCTOBER 20, 2020

MD Anderson has historically collaborated with biotechs and pharma companies to conduct cancer therapy research. This is where biotechs are essential to take promising discoveries from the research lab into a product that can be tested, approved and taken to market. But now they’ll be choosing the therapies themselves. .

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The Pharma Data

DECEMBER 17, 2020

He previously served as vice president, for drug device industrialization at AbbVie, where he led product scale-up and industrialization projects for drug-device combinations. Prior to that, Kurtz held a number of leadership positions at various companies, including Monsanto, Nektar Therapeutics, Alza Corporation, Alexza and Novo Nordisk.

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Delveinsight

AUGUST 4, 2021

With the continuous efforts by the pharma companies over the years, the therapeutic landscape for Parkinson’s Disease looks promising with several therapies in Phase II and Phase III of the clinical development. The key companies in the Migraine medical devices segment include Cefaly, Neurolief Ltd., Multiple Sclerosis.

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