Remove tag world-without-disease
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bluebird bio wins back-to-back landmark FDA approvals for first-in-class gene therapies

Pharmaceutical Technology

Skysona is indicated as a one-time gene therapy to slow the progression of cerebral adrenoleukodystrophy (CALD), a rare paediatric neurodegenerative disease in boys aged 4–17 years diagnosed with early-stage CALD. These approvals represent crucial milestones for bluebird bio, the gene therapy field, and patients with rare genetic diseases.

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Cancer research drugs: Where is the innovation?

Drug Discovery World

Click’ chemistry used to tag proteins made by cancer cells. A new method to study the proteins released by cells, which could lead to new biomarkers for diseases including cancer, has been developed by scientists at the Francis Crick Institute and Imperial College London. . appeared first on Drug Discovery World (DDW).

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Statement on Omicron sublineage BA.2

The Pharma Data

As part of its on-going work to track variants, WHO’s Technical Advisory Group on SARS-CoV-2 Virus Evolution ( TAG-VE ) met yesterday to discuss the latest evidence on the Omicron variant of concern, including its sublineages BA.1 2 may cause more severe disease in hamsters compared to BA.1. Reinfection with BA.2

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The FDA and Aduhelm: WTF?

World of DTC Marketing

Without a total overhaul of this dysfunctional status quo, it won’t be the last. Not to mention the $56,000 annual price tag. So far, no method of breaking down/removing amyloid plaques has been shown to prevent symptomatic Alzheimer’s disease in humans. </em> appeared first on World of DTC Marketing.com.

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You can’t afford to get cancer

World of DTC Marketing

As cancer survival rates rise, so do the price tags of life-saving treatments. Compare that with, say, treating heart disease. Many cancer patients without adequate insurance have only the starkest choice: your money or your life. appeared first on World of DTC Marketing.com. billion included out-of-pocket costs of $16.22

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Oslo Medicines Initiative asks how to balance innovation incentivisation with security of access

pharmaphorum

“Access to medicines remains one of the most challenging policy areas in every country we work with through the pan-European region,” said Natasha Muscat, Director of Country Health Policies and Systems at World Health Organization (WHO) Europe. Flawed funding model.

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Clover biopharmaceuticals raises $230 M; BrainStorm after ALS; BARDA grants $5.65 M LightDeck for SARS-CoV-2 antigen test; Libtayo for first-line advanced NSCLC subset

Delveinsight

The company develops transformative biologics including vaccines and therapeutics for the world’s most debilitating diseases. The company plans to use the capital to expand its pipeline of protein-based vaccines and biologic cancer therapies utilizing its innovative and proprietary Trimer-Tag technology platform.