tag metabolic-disease 
Drug Discovery World
OCTOBER 31, 2023
The children will continue to receive enzyme replacement therapy during treatment, but once the gene therapy begins to work, the research team say part of the trial aims to remove the need for weekly enzyme replacement therapy over the child’s lifetime, while the other aim is to safely target the brain disease suffered by these patients.
XTalks
OCTOBER 26, 2021
After initial rejection from the National Institute for Health and Care Excellence (NICE) last year, the non-departmental public body of the Department of Health in England has now given the green light to the gene silencing treatment Givlaari (givosiran) for the treatment of the rare metabolic disorder, acute intermittent porphyria (AIP).
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Rethinking Clinical Trials
DECEMBER 6, 2022
Director, Cardiovascular and Metabolism Research, DCRI. Making lifestyle changes is difficult especially for people living with chronic diseases, where healthy behaviors could make a big difference. This study asks how can we better facilitate health behaviors in patients with chronic diseases and can we leverage technology?
The Pharma Data
MARCH 16, 2022
using SNAP-tag) involves labeling cell proteins with a fluorescent dye, thereby enabling researchers to observe how proteins interact in the living cell and where in the cell they are located. “We His latest work on the development of biosensors has huge potential to benefit patients with certain metabolic diseases.”.
XTalks
OCTOBER 12, 2022
Features of blood perfusion in the brain detected by MRI now have clinical applications in central nervous system (CNS) cancers, neurodegenerative disease, cerebrovascular disease and demyelinating disease. An overview of the ASL MR perfusion technique to obtain cerebral blood flow (CBF) values.
Roots Analysis
SEPTEMBER 13, 2023
These molecules can be conjugated with various modalities, such as haptens, enzymes, isotopes, fluorescent tags, carrier proteins, polymers, particle conjugates and photoreactive molecules. Moreover, polymers, sugars, carrier proteins, lipid-conjugated peptides display the potential to act as peptide therapeutics for various diseases.
XTalks
APRIL 29, 2022
These bind to their respective receptors to increase glucose metabolism by increasing insulin secretion. Obesity is a chronic disease that requires effective treatment options, and Lilly is working relentlessly to support people with obesity and modernize how this disease is approached.
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