Drug Discovery World

APRIL 17, 2024

JMB: Hundreds of genetic diseases involve a missing or deficient protein and/or enzyme. Our approach is aimed at genetic diseases where amplifying healthy protein can offer therapeutic benefits. UCDs are a group of rare, inherited genetic diseases in which ammonia builds up to dangerous levels in the blood, due to a defective enzyme.

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Pharmaceutical Technology

SEPTEMBER 1, 2022

In the pursuit of improving patient care, the continued development of POC testing can help support future demand for rapid diagnosis and treatment, with opportunities to implement successful POC facilities expanding over the years as the technology has improved.

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Pharmaceutical Technology

DECEMBER 22, 2022

The funding will offer capital to extend Blueprint’s varied pipeline toward marketing as well as to continue seeking strategic and synergistic business development prospects. What all the ranked entities have in common is the demonstration of new concepts not just within their own business but in the sector as a whole.

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Drug Discovery World

JANUARY 30, 2024

“Dr Naldini open new doors for cures for otherwise untreatable genetic diseases with the full impact of his work still untapped”, she said. Developing more efficient and affordable alternatives is key. Developing value-based payment models that consider long-term benefits could improve access.

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Drug Discovery World

AUGUST 28, 2023

DS: What role does genetics play in autophagy? Could therapies like these treat rare genetic conditions? PH : Genetics plays an enormous role. In fact, some variants of Parkinson’s and ALS are genetic in origin. Could it be possible to prevent genetic diseases? DS: What’s next for the company’s pipeline?

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Drug Discovery World

MARCH 6, 2023

Assisted by a dedicated scientific advisor, a leadership coach and a BII business development expert, the new ventures will be guided in developing a detailed milestone plan and will be assisted in overcoming the challenges of growing a business.

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Imperical Blog

MAY 20, 2020

Dan McDonald, vice president, global business development. Imogen Cheese, Imperial director of business development, U.K. Wearables will be developed that notify patients and EMS services of precursors to adverse events. Gene counselors and genetic testing. Instead we are blasting forward at record pace.

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pharmaphorum

AUGUST 8, 2022

The GBT deal comes at a time when the market for SCD therapies is undergoing significant change, with multiple new drugs reaching the market after years of stagnation and progress also being made with genetic therapies from the likes of bluebird bio, Vertex Pharma/CRISPR Therapeutics and Precision Bio/Novartis.

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Pharmaceutical Technology

JULY 14, 2022

It is estimated that there are currently more than 7,000 orphan diseases, many of which are considered life-threatening and most of which have a genetic basis. The commercial investment required to research and develop an innovative drug, prove its safety and efficacy, and bring it to market is staggering.

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pharmaphorum

SEPTEMBER 21, 2021

“We need to ensure qualified patients are diagnosed, identified and engaged early on in drug development”. To complicate matters further, CNS conditions are often very difficult to identify, characterise and treat. Understanding the needs of underserved patients.

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Drug Discovery World

OCTOBER 18, 2023

Sara Donnelly, Director of Research Planning and Business Development at PhoenixBio USA explores why the right pre-clinical model is essential for teams wanting to advance adeno-associated virus vector-based gene therapies. Accelerate your gene therapy project Developing AAV vector-based gene therapies can be challenging.

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Drug Discovery World

JUNE 5, 2023

New approaches to partnering In this event in the Biotech track, Clive Cookson, Science Editor at the Financial Times, interviewed John McDonald, Corporate Vice President, Global R&D Business Development, Novo Nordisk. The discussion answered three main questions: What is the new direction for the company?

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Drug Discovery World

NOVEMBER 10, 2023

AH : I am Chief Business Officer for Antibody Analytics, a collaborative immunology CRO, specialising in supporting immunotherapy developers at the discovery to pre-clinical stages of the drug development process. This decision was pivotal to leading me to cancer research.

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Drug Discovery World

NOVEMBER 3, 2022

Paul Viggers , Chief Commercial Officer at TrakCel, explains how it fits into the drug discovery and development sector. . As such, there was little in both the traditional pharma and medical device supply chain processes that was a good fit for advanced therapy developers. . The catalysts . Next steps .

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The Pharma Data

OCTOBER 15, 2020

The award honors McHutchison’s work in developing life-changing and curative therapies for patients with the hepatitis C virus. The committee is tasked with supporting BeyondSpring’s business development activities related to its lead asset, Plinabulin, and other pipeline assets. BeyondSpring – BeyondSpring Inc.

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Pharmaceutical Technology

JUNE 19, 2023

Pharmaceutical companies are putting their trust in the immense potential this new generation of medicine has for treating individuals with rare genetic diseases, which currently affect an estimated 280 million patients worldwide. Cell and gene therapies are not your typical clinical supply chain. That was really a key part of the design.

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Drug Discovery World

NOVEMBER 9, 2023

The first three include: Sungjin Park, PhD, CEO, Onegene Biotechnology, on: ‘UniStac: Enzyme-mediated conjugation technology for accelerated development of tetraspecific NASH drug’. Gail Calvert, Field Application Scientist, Sartorius UK, on: ‘Leveraging integrated and advanced technologies for successful cell line development’.

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The Pharma Data

NOVEMBER 3, 2020

Nasdaq:LOGC) (LogicBio), a company dedicated to extending the reach of genetic medicine with pioneering targeted delivery platforms, announced today the U.S. Fast Track designation allows for early and frequent communication with the FDA throughout the entire drug development and review process. LEXINGTON, Mass.,

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Drug Discovery World

APRIL 25, 2023

Today’s decision by the Chancellor is a vote of confidence in the UK’s outstanding life sciences start-up community, creating the opportunities needed to develop new tests, medicines and advances in healthcare for cancer patients,” stated Tony Hickson, Chief Business Officer of Cancer Research UK (CRUK) and Cancer Research Horizons.

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The Pharma Data

DECEMBER 17, 2020

Kurtz brings more than 26 years of experience in global manufacturing, engineering, supply chain, CMC development and program management for drugs and devices at various stages of development. Cadavid will be responsible for the strategy, direction and execution of the company’s clinical development programs.

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Drug Discovery World

NOVEMBER 8, 2023

On Day 1, Tuesday 14 November 2023, the tracks include: Display of biologics, antibody-based cancer therapies, safety and efficacy of bispecific antibodies, modulating the tumour microenvironment, optimisation and developability, and cell line and systems engineering.

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The Pharma Data

DECEMBER 8, 2020

AbCellera’s AI-powered antibody discovery platform speeds the otherwise lengthy and grueling process by analyzing the database of natural immune systems to find antibodies that can be developed into drugs. Tackle the toughest problems in drug development.” The promise to partners is to “move quickly. Reduce cost. Sigilon Therapeutics

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Drug Discovery World

FEBRUARY 7, 2023

Here, DDW’s Diana Spencer takes a look at the ways ChatGPT and technology like it could change the future of drug discovery and development. Given that some universities banned it already, worrying that anyone could suddenty pass any test, I tried asking a hard scientific question requiring specific knowledge in the field of #genetics.”

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The Pharma Data

NOVEMBER 10, 2020

Furthermore, data show that the class of drug substances being developed within AlzeCure’s platform, so-called gamma-secretory modulators, selectively affect the production of toxic Abeta-amyloid, without affecting the cleavage of other substrates that potentially play an important role in normal physiological function. in the brain.

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Drug Discovery World

OCTOBER 31, 2022

DS: How has our understanding of the brain developed in the last 70 years? . Now, many next-generation CNS companies are developing therapeutics that focus on pathways similar to ketamine to enhance synaptic plasticity and restore higher-order levels of brain function and signaling.

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Drug Discovery World

APRIL 27, 2023

The abundant networking opportunities with world-class researchers here not only help grow our customer base but are also useful for recruitment or identifying potential collaborators for new software integrations or developments.” As a well- known life science hub, we will benefit from the pool of talent concentrated in RTP.

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Drug Discovery World

SEPTEMBER 6, 2022

DDW Editor Reece Armstrong looks at the cell and gene therapy landscape, examining the challenges facing developers and the trends we can expect to see throughout the year. . For cell and gene therapies, Covid-19 was a “double-edged sword”, according to Kristin Thompson, Chief Business Officer at eureKARE.

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The Pharma Data

NOVEMBER 5, 2020

Business Highlights. Key Pipeline Progress Regeneron has more than 20 product candidates in clinical development, including five marketed products for which it is investigating additional indications. Corporate and Business Development Update. Research and development (R&D). $. government. Operating Expenses.

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XTalks

OCTOBER 1, 2020

And although academia and industry have often been pitted against each other in the realm of scientific discovery and development, there may be more similarities and synergies between the two than we may think. WeiQi Lin, MD, PhD, executive vice president of research & development and principal scientist, DURECT Corporation.

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pharmaphorum

DECEMBER 14, 2022

One of the fund’s latest investments is in Extend, a new joint venture between Evotec, CDP Venture Capital, and Angelini Ventures which will leverage the best of scientific research from Italian academic institutions to support the development and commercialisation of promising therapeutics.

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The Pharma Data

OCTOBER 26, 2020

V590 — a SARS-CoV-2 vaccine candidate in development in collaboration with the International AIDS Vaccine Initiative (IAVI) that uses a recombinant vesicular stomatitis virus (rVSV) platform, the same platform used for Merck’s approved Ebola Zaire virus vaccine, will enter Phase 1 development shortly.

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Pharmaceutical Technology

MARCH 20, 2023

In APAC, for example, industry commentators are predicting that the pharmaceutical sector’s historic focus on genetics and manufacturing will shift towards cutting-edge technology. Against this backdrop, new specialisations are cropping up in regional investment activity and cash raising techniques. Source: GlobalData.

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Pharmaceutical Technology

MARCH 20, 2023

It’s home to the highest genetic diversity of humans on the planet and it’s filled with potential participants who are more and more urbanised and eager to be part of the clinical trials.” However, Africa currently accounts for a very low percentage of global clinical trials, with estimates putting it at approximately 2.5%.

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Pharmaceutical Technology

MAY 9, 2023

For Jamaels, whose track record in managing complex operations and delivering process improvements spans GSK Vaccines and one of the world’s largest companies, GE, the technological shift is an exciting development: “I’m passionate about the digital transformation that our industry is going through,” he says.

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