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Sickle Cell Disease: The Importance of Amplifying Patient Voices

Advarra

Red blood cells contain hemoglobin, a protein that carries oxygen. These are reasons for biotech organizations to renew a focus on improving diversity in clinical research while bringing more sickle cell gene therapies to market. A visit to a podiatrist and family doctor yielded less than satisfactory diagnoses.

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Suppressing the spread of tumors

The Pharma Data

While the cancer cells containing MFSD1 quickly died under the mechanical stress, those without the protein tended to remain intact. To optimize therapy for their patients, doctors are already analyzing the expression of certain genes. Now, they can also look for the gene encoding the protein MFSD1.

Protein 40
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Improving Access to Cures Through Innovation

Pfizer

on the policies of foreign governments — and could alter how doctors and patients access drugs. Pfizer and Sangamo Therapeutics Announce Phase 3 Trial of Investigational Gene Therapy for Hemophilia A Has Re-Opened Recruitment. Promote market competition and protect innovation by rejecting foreign price controls on prescription drugs.

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A Comprehensive Guide to Atopic Dermatitis

Olympian Clinical Research

If you are experiencing any of the above symptoms, it is important to consult with your doctor or dermatologist for an accurate diagnosis. This condition occurs when a gene variation causes the skin to become dry and irritated. Talk to your doctor about prescription medications that may help relieve itching and inflammation.

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Searching for answers in rare epilepsy

pharmaphorum

Charlie has spent more than 26 years working on the human genome – 22 of which were spent at the Wellcome Sanger Institute, helping to assemble the human genome and trying to understand the function of the genes contained within it. Shortly after that, she started making jackknife movements.

Genome 86
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Searching for answers in rare epilepsy

pharmaphorum

Charlie has spent more than 26 years working on the human genome – 22 of which were spent at the Wellcome Sanger Institute, helping to assemble the human genome and trying to understand the function of the genes contained within it. Shortly after that, she started making jackknife movements.

Genome 73
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Top Life Science News and Trends in 2023 at Xtalks

XTalks

Novo Nordisk’s GLP-1 weight loss-specific drug Wegovy (semaglutide) has been facing similar shortages, as it contains the same active ingredient as Ozempic. The shortages have been partly blamed on the off-label prescribing of the drugs for weight loss. The year 2023 was filled with some remarkable news and advancements in the life sciences.