Pharmaceutical Technology

FEBRUARY 9, 2023

ReviR Therapeutics chief scientific officer Paul August said: “Asieris is a global biopharma company specialised in the development of GU oncology therapies, and we are excited to be working with them to discover new treatments for indications of interests. Cell & Gene Therapy coverage on Pharmaceutical Technology is supported by Cytiva.

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Worldwide Clinical Trials

OCTOBER 24, 2023

Savvy patients make for great partners Even when a rare disease is in the earlier stages of being understood, patients and their advocates draw on lessons from other rare communities to focus on strategic approaches to meet their goals effectively and efficiently. Over the years, I have attended several Global Genes Summits.

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Worldwide Clinical Trials

APRIL 3, 2024

Partnering with advocacy organizations can help them to explain radiopharmaceuticals to their members and encourage participation. Moreover, partnering with a CRO that has experts with specialized knowledge in radiopharmaceuticals is critical, as it can streamline the regulatory process.

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XTalks

MARCH 29, 2024

Xtalks spoke to Andrea Li, head of Canadian operations at Too Good To Go, to learn valuable insights into how the company is changing the landscape of food sustainability. The guiding principles for how I thought about my career have always been around this theme called Tech for Good, as I’d call it,” Li says. “So

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Pharmaceutical Technology

MARCH 28, 2023

Vertex Pharmaceuticals Cell and Genetic Therapies chief and executive vice-president Bastiano Sanna said: “We have multiple programmes in our T1D portfolio including VX-880 and VX-264, which are in the clinic, as well as our hypoimmune programme, in preclinical development.

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Pharmaceutical Technology

MARCH 1, 2023

Tevard CEO and co-founder Daniel Fischer said: “Given Vertex’s proven track record of developing novel therapies to treat serious disease, we’re thrilled to partner with them on this important effort. “By

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Pharmaceutical Technology

MAY 19, 2023

Led by Hatteras Investment Partners, the financing round has seen participation from existing investors, including 8VC, Alexandria Venture Investments and Newpath Partners, along with new investors Moore Strategic Ventures and ARCH Venture Partners.

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Worldwide Clinical Trials

APRIL 25, 2024

Here, we delve into how these challenges can be navigated with the aid of clinical assessment services, leveraging the expertise of Worldwide Clinical Trials’ Clinical Assessments Technologies (CAT) team. However, further improvements are needed , including: Refinement of trial designs that address specific factors (e.g.,

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ACRP blog

MARCH 26, 2024

Clinical research lacks workers — but through the functional service provider (FSP) model, we’re training the professionals we need. But as we build current FSP teams, Parexel is moving away from an acquisition-only approach. In order to meet our partners’ fluctuating and often urgent staff needs, we’ve expanded our strategy.

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Pharmaceutical Technology

DECEMBER 21, 2022

We look forward to being part of the UK’s world-renowned science and innovation community, contributing to the UK health ecosystem through significant investments in R&D activities and expanding our clinical trial footprint across the country.”.

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Pharmaceutical Technology

DECEMBER 5, 2022

According to the latest deal, the University of Queensland (UQ) and Griffith University will serve as foundational partners. We want the world to know that Queensland is where business can come to do science, and science can come to do business.”.

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Pharmaceutical Technology

DECEMBER 8, 2022

This guide addresses how cell thawing has historically developed into the new techniques used today, along with the physical and biological implications of key metrics and components such as warming rate and ice structure.

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Pharmaceutical Technology

DECEMBER 23, 2022

ProQR founder and CEO Daniel de Boer said: “Our original collaboration with Lilly, which leverages our Axiomer RNA editing technology platform, continues to progress well and we are pleased to be expanding our partnership to include additional targets, along with an option for Lilly to opt in for more.”.

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Rethinking Clinical Trials

JULY 18, 2023

Natalia Morone In an interview at the annual NIH Pragmatic Trials Collaboratory Steering Committee meeting, Dr. Lynn DeBar and Dr. Natalia Morone had a conversation about sharing trial results with participant partners. “I think we have that responsibility.” “I think we have that responsibility.”

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Pharmaceutical Technology

APRIL 27, 2023

Orbital Therapeutics has raised $270m in a Series A round led by ARCH Venture Partners to advance a portfolio of programmable RNA therapeutics. The initial investors were a16z Bio + Health and Newpath Partners.

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Intouch Solutions

APRIL 1, 2024

March is a month of empowerment, reflection, and celebration as we recognize Women’s History Month. In this MasterClass, she taught attendees how they can make an impact at any level. By fostering a culture of inclusivity, empowerment, and support, we continue to pave the way for a more equitable and prosperous future for all.

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Pharmaceutical Technology

APRIL 14, 2023

Ginkgo will partner with researchers from Wisconsin-Madison to discover new and improved GD2 CAR designs with improved persistence, fitness and proliferation. The company can use its mammalian cell engineering expertise and capabilities to screen CAR T-cells, to discover and optimise next-generation therapeutic candidates for its partners.

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Pharmaceutical Technology

MARCH 10, 2023

The representative said NHSBT plans to continue increasing manufacturing capacity in this way and said, “We are actively pursuing collaborations with external partners.”

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Pharmaceutical Technology

APRIL 21, 2023

Moderna CEO Stéphane Bancel said: “Since our inception, we have always strived to be at the forefront of cutting-edge technology, leveraging innovations to deliver the greatest possible impact to people through mRNA medicines. “We Cell & Gene Therapy coverage on Pharmaceutical Technology is supported by Cytiva.

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Rethinking Clinical Trials

FEBRUARY 7, 2024

Food and Drug Administration (FDA) Commissioner Robert Califf asked the Reagan-Udall Foundation to conduct research and consult with experts to better understand how consumers find, consume, and perceive health information, especially regarding FDA-regulated products. How do people want to hear that science is a moving target?

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Pharmaceutical Technology

NOVEMBER 30, 2022

Rocky Mountain Labs will partner to select the saRNA vaccine candidates for CCHFV. HDT Bio CEO Steve Reed said: “We are grateful to DOD and HHS for their support. “We We look forward to working with our partners and the MCDC to protect our military personnel and the American people as a whole from biological threats.”.

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Rethinking Clinical Trials

JULY 12, 2023

The supplement was an opportunity to better understand what data sharing policies exist and how well they align with pragmatic trials. “We suspected that pragmatic clinical trials might raise different challenges compared to sharing data from traditional explanatory trials,” she explained.

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Pharmaceutical Technology

FEBRUARY 23, 2023

Under the deal, both companies will partner on the research and preclinical studies, which will be funded by Moderna. This guide addresses how cell thawing has historically developed into the new techniques used today, along with the physical and biological implications of key metrics and components such as warming rate and ice structure.

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Worldwide Clinical Trials

JANUARY 24, 2024

Many of the rare disease studies we support at Worldwide have a genetic etiology, and we discuss genetics and genetic testing with these sponsors. Much of what we discuss I covered in my presentation, “Leveraging Genetics to Support Rare Disease Clinical Trials,” at last year’s World Orphan Drug Congress (WODC) EU.

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Worldwide Clinical Trials

FEBRUARY 26, 2024

But how can the patient experience be leveraged to drive your trial’s success? In our recent Xtalks webinar, “ See How It’s Done: Case Studies on Patient Experience Design ,” our Therapeutic Strategy Lead, Rare Disease, Juliane K. Find out how he solved them by challenging the traditional structure in the full webinar.

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Clinical Trials Clinical Trials Trials Clinical Research 137

World of DTC Marketing

FEBRUARY 3, 2022

It won’t be easy and means changing the mindset from a vendor to a strategic partner. 5ive: We want to know about your target market. Demographics alone don’t mean a damn thing; we need psychographics. 6ix: We have the analytics people to show you what works; here’s why that’s important.

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Marketing Pharma Production Production Doctors 247

XTalks

MARCH 27, 2024

The collaboration between IVD manufacturers and lab testing partners is central to precise and efficient diagnostic processes. To delve deeper into this subject, Xtalks spoke with Dr. Dhiman unraveled the complexities of the IVD field, highlighting the importance of collaboration between IVD manufacturers and lab testing partners.

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Pharmaceutical Technology

JANUARY 20, 2023

In a panel discussion on the “State of the Pandemic” , Bancel said, “We’ve shown this summer that we are able to adapt to different variants very quickly”. Increasing manufacturing capacity for pandemic prevention “The other piece we are working on is … how do we build manufacturing capacity around the world?”,

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Pharmaceutical Technology

MAY 25, 2023

New investors included research and development partner Novo Nordisk, Lee Family Office (Asia) and Woodline. This guide addresses how cell thawing has historically developed into the new techniques used today, along with the physical and biological implications of key metrics and components such as warming rate and ice structure.

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Rethinking Clinical Trials

SEPTEMBER 28, 2023

How might we better structure preventive visits? From the beginning we did not know what the intervention was going to be. As we went to each new clinical space there were things we could not have anticipated that they wanted to change for their clinic. Learn more Read more about PARENT in JAMA.

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Pharmaceutical Technology

DECEMBER 18, 2022

We are grateful to the CHMP for their review of our submission and look forward to an authorisation decision from the European Commission.”. By downloading this Whitepaper, you acknowledge that we may share your information with our white paper partners/sponsors who may contact you directly with information on their products and services.

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Pharmaceutical Technology

JANUARY 12, 2023

We believe the advanced RNA technology and human disease models of Phlox Therapeutics perfectly partner with the delivery tools Solid Biosciences brings to this collaboration.”. The post Solid Biosciences partners with Phlox for cardiac disease therapies appeared first on Pharmaceutical Technology.

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RNA Gene Therapy Genetics Genetic Disease 130

Drug Discovery World

APRIL 25, 2024

Xaira Therapeutics, a joint incubation by ARCH Venture Partners and Foresite Labs, has launched with more than $1 billion of committed capital from lead investors. Now, witnessing how AI is impacting other industries and the considerable progress in applications of AI in biology, I believe we are poised for a revolution.”

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Pharmaceutical Technology

JANUARY 10, 2023

By using data from patients for patients, we aim to discover the best immunogenic targets for multiple tumour indications and across patient populations.” . Boehringer Ingelheim Cancer Immunology + Immune Modulation global head Lamine Mbow said: “At Boehringer Ingelheim, we are committed to transforming patients’ lives.

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Drug Discovery World

OCTOBER 24, 2023

MP : Lithuania is a hub of gene editing, as we not only have the Life Sciences Centre at Vilnius University, but also the European Molecular Biology Laboratory (EMBL). We never went through rounds of investments like most companies. How has the company had to change over the years? DS: CRISPR is constantly evolving.

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Rethinking Clinical Trials

APRIL 4, 2023

The guides serve as annotated tables of contents, pointing readers to essential content in the Living Textbook to help successfully launch an ePCT and partner with healthcare systems leaders. We are excited to share this new tool with the research community,” said Tammy Reece, project director for the NIH Collaboratory Coordinating Center.

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Pharmaceutical Technology

NOVEMBER 29, 2022

Neogene’s leading TCR discovery capabilities and extensive manufacturing experience complement the cell therapy capability we have built over the last three years and allow us to accelerate the development of potentially curative cell therapies for the benefit of patients.”.

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