Remove therapeutic-depth cell-and-gene-therapy
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Astellas Pharma signs licence deal with Kate Therapeutics for KT430

Pharmaceutical Technology

Astellas Pharma (Astellas) has entered an exclusive licence deal with Kate Therapeutics (KateTx) to develop and commercialise KT430. KT430 is a preclinical, next-generation investigational gene therapy designed for the treatment of X-linked myotubular myopathy (XLMTM), a rare and life-threatening neuromuscular disease.

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Forge receives QP declaration to manufacture AAV gene therapies in Europe

Pharmaceutical Technology

Forge Biologics has received a qualified person (QP) declaration to manufacture adeno-associated virus (AAV) gene therapies to support European clinical programmes. The company stated that a European QP has completed an in-depth audit at its manufacturing facility in Columbus, Ohio, US.

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Can vertical AI advance cell and gene therapies? 

Drug Discovery World

Andrew Busey , Co-Founder, Form Bio discusses why vertical AI is set to reshape the cell and gene therapy sector. The cell and gene therapy industry is no exception to this digital transformation. Here’s what this means for pharmaceutical leaders and patients.

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Rare Disease Spotlight – tracing the rise of orphan drug designations over almost 40 years

Pharmaceutical Technology

This year has already been eventful when it comes to the development of therapies for rare diseases. Additionally, pricing and access for rare disease therapies continue to be scrutinized closely. Additionally, pricing and access for rare disease therapies continue to be scrutinized closely.

Drugs 246
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International Women’s Day 2024: A Spotlight on 5 Women’s Health Webinars with Xtalks

XTalks

International Women’s Day 2024 is Friday, March 8, and this year’s theme is “ Inspire Inclusion ,” which encourages a collective effort to understand, value and advocate for women’s inclusion across all spheres of life. A significant 58 percent of women worldwide have heightened their use of supplements to support overall wellness.

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iPSC Manufacturing Summit

pharmaphorum

With iPSCs exhibiting game-changing potential in the bid to develop an off-the-shelf therapy, the brand-new iPSC Manufacturing Summit is the only summit dedicated to solving the manufacturing, quality and analytical challenges hindering your iPSC-derived treatments from reaching patients. Hear from: Fate Therapeutics. Cartherics.

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IN FOCUS: Solvias

Pharmaceutical Technology

The move is particularly timely given the significant growth expected in global sales of cell and gene therapies. M&A – Commended PRODUCT LAUNCHES – Commended RESEARCH AND DEVELOPMENT – Commende d. Pharmaceutical Technology Excellence Rankings – The Verdict.